A phase Ib, open-label, ascending dose study with step-up doses to assess safety, tolerability, and pharmacokinetics of PIT565 in participants with systemic lupus erythematosus (SLE)

2023-510025-14-00 Protocol CPIT565B12101 Human pharmacology (Phase I) - Other Ongoing, recruitment ended

Start 8 Oct 2024 · Status Ongoing, recruitment ended · 5 EU/EEA countries · 10 sites · Protocol CPIT565B12101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Ongoing, recruitment ended
Participants planned 44
Countries 5
Sites 10

Systemic Lupus Erythematosus

Key facts

Sponsor
Novartis Pharma AG
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Immune System Diseases [C20]
Trial duration
8 Oct 2024 → ongoing
Decision date (initial)
2024-09-16
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

External identifiers

EU CT number
2023-510025-14-00
ClinicalTrials.gov
NCT06335979

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Systemic Lupus Erythematosus

VersionLevelCodeTermSystem organ class
21.1 PT 10042945 Systemic lupus erythematosus 100000004859

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Novartis Pharma AG

Sponsor organisation
Novartis Pharma AG
Address
Lichtstrasse 35
City
Basel
Postcode
4056
Country
Switzerland

Scientific contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Public contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Locations

5 EU/EEA countries · 10 investigational sites

By country

CountryMS statusPlanned subjectsSites
Bulgaria Ended 3 1
Germany Ongoing, recruiting 16 3
Hungary Ongoing, recruiting 4 2
Netherlands Ongoing, recruiting 4 1
Spain Ongoing, recruiting 5 3
Rest of world
United States, China, Switzerland
12

Investigational sites

Bulgaria

1 site · Ended
Medical Center Comac Medical Ltd.
#1004, Ulitsa Urvich 13, Krasno Selo District, Sofia

Germany

3 sites · Ongoing, recruiting
Universitaetsklinikum Essen AöR
1014:Klinik für Nephrologie und Infektiologie, Hufelandstrasse 55, Holsterhausen, Essen
Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR
1002: I. Medizinische Klinik und Poliklinik, Langenbeckstrasse 1, Oberstadt, Mainz
Charite Research Organisation GmbH
1001, Chariteplatz 1, Mitte, Berlin

Hungary

2 sites · Ongoing, recruiting
University Of Szeged
1010: Szent-Györgyi Albert Klinikai Központ, Klinikai Farmakológiai Központ, Fázis I. vizsgálóhely, Koranyi Fasor 6, 6720, Szeged
Semmelweis University
1011: Belgyógyászati és Onkológiai Klinika, Klinikai Farmakológiai részleg, Koranyi Sandor Utca 2/a, Kerulet, Budapest VIII

Netherlands

1 site · Ongoing, recruiting
Centre for Human Drug Research
#1003: Internal Medicine, Zernikedreef 8, 2333 CL, Leiden

Spain

3 sites · Ongoing, recruiting
Hospital Universitari Vall D Hebron
#1005: Rheumatology, Passeig De La Vall D'Hebron 119-129, 08035, Barcelona
Hospital Universitario Ramon Y Cajal
#1013; Rheumatology, Carretera Del Colmenar Viejo Km 9 100, Por El Pardo, Madrid
Complexo Hospitalario Universitario De Santiago
#1006: Rheumatology, Calle Choupana Da S/n, 15706, Santiago De Compostela

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Bulgaria 2024-11-07 2024-11-25 2024-11-07 2024-11-07
Germany 2024-10-08 2024-10-08
Hungary 2026-04-21 2026-04-21
Netherlands 2025-02-20 2025-02-20
Spain 2024-10-31 2024-10-31

Application history

9 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-05-17 Germany Acceptable
2024-09-09
2024-09-09
2 NON SUBSTANTIAL MODIFICATION NSM-1 2024-09-19 Acceptable
2024-09-09
2024-09-19
3 NON SUBSTANTIAL MODIFICATION NSM-2 2024-09-26 Acceptable
2024-09-09
2024-09-26
4 SUBSTANTIAL MODIFICATION SM-2 2024-10-11 Acceptable 2024-10-24
5 SUBSTANTIAL MODIFICATION SM-1 2024-10-17 Germany Acceptable 2024-11-15
6 SUBSTANTIAL MODIFICATION SM-3 2025-01-08 Germany Acceptable
2025-03-10
2025-03-10
7 SUBSEQUENT ADDITION OF MSC APP-7 2025-06-04 2025-08-22
8 SUBSTANTIAL MODIFICATION SM-4 2025-09-10 Germany Acceptable
2025-11-03
2025-11-05
9 SUBSTANTIAL MODIFICATION SM-5 2026-02-12 Germany Acceptable
2026-04-14
2026-04-15