Phase IB open label, long-term, extension basket trial of RAY121 to inhibit classical complement pathway in immunological diseases (RAINBOW-LTE trial)

2024-511346-39-00 Protocol RAY903CT Human pharmacology (Phase I) - Other Authorised, recruiting

Start 28 Mar 2025 · Status Authorised, recruiting · 14 EU/EEA countries · 43 sites · Protocol RAY903CT

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Authorised, recruiting
Participants planned 144
Countries 14
Sites 43

Immune-mediated necrotizing myopathy

Key facts

Sponsor
Chugai Pharmaceutical Co. Ltd.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Skin and Connective Tissue Diseases [C17]
Trial duration
28 Mar 2025 → ongoing
Decision date (initial)
2025-02-17
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Immune-mediated necrotizing myopathy

VersionLevelCodeTermSystem organ class
20.0 PT 10012503 Dermatomyositis 100000004858
20.0 PT 10034277 Pemphigoid 100000004858
20.0 PT 10004213 Behcet's syndrome 100000004866
23.0 LLT 10083567 Immune-mediated thrombocytopenia 10005329
22.1 PT 10083073 Immune-mediated myositis 100000004859
23.0 LLT 10083567 Immune-mediated thrombocytopenia 10005329
20.0 PT 10002817 Antiphospholipid syndrome 100000004851

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Chugai Pharmaceutical Co. Ltd.

Sponsor organisation
Chugai Pharmaceutical Co. Ltd.
Address
1-1 Nihonbashi-Muromachi 2-Chome, Chuo-ku Chuo-ku
City
Chuo
Postcode
103-8324
Country
Japan

Scientific contact point

Organisation
Chugai Pharmaceutical Co. Ltd.
Contact name
Clinical trials information

Public contact point

Organisation
Chugai Pharmaceutical Co. Ltd.
Contact name
Clinical trials information

Locations

14 EU/EEA countries · 43 investigational sites

By country

CountryMS statusPlanned subjectsSites
Austria Authorised, recruitment pending 4 1
Bulgaria Authorised, recruiting 6 3
Croatia Authorised, recruitment pending 6 6
Czechia Authorised, recruitment pending 2 1
France Ongoing, recruiting 10 2
Germany Authorised, recruitment pending 9 6
Hungary Authorised, recruitment pending 7 2
Italy Authorised, recruitment pending 2 3
Netherlands Authorised, recruitment pending 6 2
Norway Ongoing, recruiting 2 3
Poland Ongoing, recruiting 4 1
Portugal Authorised, recruitment pending 3 2
Romania Ongoing, recruiting 7 2
Spain Authorised, recruitment pending 10 9
Rest of world
Taiwan, Turkey, Australia, Canada, Japan
66

Investigational sites

Austria

1 site · Authorised, recruitment pending
Medical University Of Vienna
Department of Clinical Pharmacology, Waehringer Guertel 18-20, Alsergrund, Vienna

Bulgaria

3 sites · Authorised, recruiting
University Multiprofile Hospital For Active Treatment St. Ivan Rilski EAD
Clinic of Rheumatology, Ulitsa Urvich 13, 1612, Sofia
Specialized Hospital For Active Treatment Of Hematological Diseases EAD
Clinic of Clinical Hematology, Bulevard Kliment Ohridski 1a, 1797, Sofiya
Umbal - Prof. D-R Stoyan Kirkovich AD
Department of Clinical Hematology, Ulitsa General Stoletov 2, 6003, Stara Zagora

Croatia

6 sites · Authorised, recruitment pending
Specijalna Bolnica Medico
Clinical pharmacology, Agaticeva 8, 51000, Rijeka
Klinicki bolnicki centar Sestre milosrdnice
Dermatovenerology, Vinogradska Cesta 29, Zagreb, Grad Zagreb
KBC Zagreb
Immunodermatology, Ulica Mije Kispatica 12, Zagreb, Grad Zagreb
Specijalna Bolnica Medico
Rheumatology, Agaticeva 8, 51000, Rijeka
Specijalna Bolnica Medico
Hematology, Agaticeva 8, 51000, Rijeka
Specijalna Bolnica Medico
Dermatology and Venerology, Agaticeva 8, 51000, Rijeka

Czechia

1 site · Authorised, recruitment pending
Fakultni Nemocnice Kralovske Vinohrady
Dermatovenerologická klinika, Srobarova 1150/50, Vinohrady, Prague

France

2 sites · Ongoing, recruiting
Centre Hospitalier Universitaire De Montpellier
Rheumatology, 80 Avenue Augustin Fliche, 34295, Montpellier Cedex 5
Hopitaux Universitaires Pitie Salpetriere
Internal Medicine and Clinical Immunology, 47 To 83 Boulevard De L Hopital, 75013, Paris

Germany

6 sites · Authorised, recruitment pending
Immanuel Klinik Ruedersdorf
Neurologie, Seebad 82, 15562, Rüdersdorf
Universitaetsklinikum Tuebingen AöR
Hautklinik, Liebermeisterstrasse 25, Innenstadt, Tuebingen
Universitaetsmedizin Goettingen
Klinik für Neurologie, Robert-Koch-Strasse 40, Weende, Goettingen
Universitaetsklinikum Erlangen AöR
Hautklinik, Ulmenweg 18, Innenstadt, Erlangen
Technische Universitaet Dresden
Klinik und Poliklinik für Dermatologie, Fetscherstrasse 74, Johannstadt-Nord, Dresden
Universitaetsklinikum Schleswig-Holstein AöR
Institut für Entzündungsmedizin, Ratzeburger Allee 160, 23538, Luebeck

Hungary

2 sites · Authorised, recruitment pending
Semmelweis University
Belgyógyászati és Onkológiai Klinika, Koranyi Sandor Utca 2/a, Kerulet, Budapest VIII
University Of Szeged
Szent-Györgyi Albert Klinikai Központ, Klinikai Farmakológiai Központ Fázis I. Vizsgálóhely, Koranyi Fasor 6, 6720, Szeged

Italy

3 sites · Authorised, recruitment pending
Humanitas Mirasole S.p.A.
Dermatology, Via Alessandro Manzoni 56, 20089, Rozzano
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Oncologia ed Ematologia Clinica e Sperimentale, Via Piero Maroncelli 40, 47014, Meldola
Ospedale San Giovanni Bosco
SCdU Nefrologia e Dialisi, Piazza Del Donatore Di Sangue 3, 10154, Turin

Netherlands

2 sites · Authorised, recruitment pending
Universitair Medisch Centrum Groningen
Dermatology, Hanzeplein 1, 9713 GZ, Groningen
Universitair Medisch Centrum Utrecht
Haematology, Heidelberglaan 100, 3584 CX, Utrecht

Norway

3 sites · Ongoing, recruiting
Helse Stavanger HF
Rheumatology, Gerd-Ragna Bloch Thorsens Gate 8, 4011, Stavanger
Sorlandet Sykehus HF
Rheumatology, Egsveien 100, 4615, Kristiansand S
Sykehuset Oestfold HF Kalnes
Hematology, Kalnesveien 300, 1714, Graalum

Poland

1 site · Ongoing, recruiting
Narodowy Instytut Geriatrii Reumatologii I Rehabilitacji Im Prof. Dr Hab. Med. Eleonory Reicher
Centrum Wsparcia Badań Klinicznych, Ul. Spartanska 1, 02-637, Warsaw

Portugal

2 sites · Authorised, recruitment pending
Unidade Local De Saude De Gaia/Espinho E.P.E.
Rheumatology, Rua Conceicao Fernandes S/n, 4434-502, Vila Nova De Gaia
CCAB Centro Clinico Academico Braga Associacao
Rheumatology, Lugar De Sete Fontes S Victor, 4710-243, Braga

Romania

2 sites · Ongoing, recruiting
Arensia Clinics S.R.L.
Internal Medicine, Intrarea Tudor Stefan 38-40, 011658, Bucharest
Institute Of Oncology Prof. Dr. Ion Chiricuta Cluj-Napoca
Internal Medicine, Strada Republicii 34-36, 400015, Cluj-Napoca

Spain

9 sites · Authorised, recruitment pending
Clinica Universidad De Navarra
Hematology, Calle Marquesado De Santa Marta 1, 28027, Madrid
Hospital Universitari Vall D Hebron
Hematology, Passeig De La Vall D'Hebron 119-129, 08035, Barcelona
Clinica Universidad De Navarra
Hematology, Pio XII Etorbidea 36, 31008, Pamplona
Hospital Universitario Y Politecnico La Fe
Hematology, Avenida De Fernando Abril Martorell 106, 46026, Valencia
Hospital Universitari Vall D Hebron
Internal Medicine, Passeig De La Vall D'Hebron 119-129, 08035, Barcelona
Hospital Universitario Reina Sofia
Rheumatology, Avenida Menendez Pidal S/n, 14004, Cordoba
University Hospital Virgen Del Rocio S.L.
Hematology, Avenida De Manuel Siurot S/n, 41013, Sevilla
Hospital Universitario 12 De Octubre
Rheumatology, Avenida De Cordoba Sn, 28041, Madrid
Hospital Universitario Ramon Y Cajal
Rheumatology, Carretera Del Colmenar Viejo Km 9 100, Por El Pardo, Madrid

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Bulgaria 2026-04-14
France 2025-04-02 2025-04-29
Norway 2026-03-06 2026-03-26
Poland 2025-04-02 2025-10-02
Romania 2025-03-28 2025-08-25

Application history

9 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-10-07 Austria Acceptable
2025-02-10
2025-02-11
2 NON SUBSTANTIAL MODIFICATION NSM-1 2025-02-20 Acceptable
2025-02-10
2025-02-20
3 NON SUBSTANTIAL MODIFICATION NSM-2 2025-02-25 Acceptable
2025-02-10
2025-02-25
4 SUBSTANTIAL MODIFICATION SM-1 2025-03-03 Acceptable 2025-03-27
5 SUBSTANTIAL MODIFICATION SM-2 2025-03-05 Acceptable 2025-03-19
6 SUBSTANTIAL MODIFICATION SM-3 2025-06-06 Austria Acceptable
2025-07-16
2025-07-17
7 NON SUBSTANTIAL MODIFICATION NSM-3 2025-09-09 Acceptable
2025-07-16
2025-09-09
8 SUBSTANTIAL MODIFICATION SM-4 2025-11-03 Acceptable 2025-11-11
9 NON SUBSTANTIAL MODIFICATION NSM-4 2026-02-11 Austria Acceptable 2026-02-11