A Study to Investigate the Safety and Efficacy of KQB198 as Monotherapy and in Combination in Participants with Advanced Hematologic Malignancies

2024-511457-22-00 Protocol KQB198-102 Human pharmacology (Phase I) - Other Authorised, recruiting

Start 30 Jan 2025 · Status Authorised, recruiting · 6 EU/EEA countries · 18 sites · Protocol KQB198-102

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Authorised, recruiting
Participants planned 129
Countries 6
Sites 18

Advanced Hematologic Malignancies

Key facts

Sponsor
Kumquat Biosciences Inc.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
30 Jan 2025 → ongoing
Decision date (initial)
2025-01-15
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

External identifiers

EU CT number
2024-511457-22-00
WHO UTN
U1111-1309-0750

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Advanced Hematologic Malignancies

VersionLevelCodeTermSystem organ class
21.1 LLT 10066481 Hematological malignancy 10029104

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Kumquat Biosciences Inc.

Sponsor organisation
Kumquat Biosciences Inc.
Address
10770 Wateridge Circle
City
San Diego
Postcode
92121-5805
Country
United States

Scientific contact point

Organisation
Kumquat Biosciences Inc.
Contact name
Regulatory Submissions

Public contact point

Organisation
Kumquat Biosciences Inc.
Contact name
Regulatory Submissions

Locations

6 EU/EEA countries · 18 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ended 12 3
Germany Ended 12 2
Italy Ongoing, recruitment ended 15 4
Netherlands Ended 9 1
Poland Ongoing, recruitment ended 12 4
Spain Ongoing, recruitment ended 9 4
Rest of world
United Kingdom, Australia, United States
60

Investigational sites

France

3 sites · Ended
CHU de Tours - Hopital Bretonneau
Hematology, 2 boulevard Tonnellé, 37044, Tours Cedex 01
Centre Leon Berard
Medical oncology, 28 Rue Laennec, 69008, Lyon
Hôpital de la Timone
Centre d'Essais Précoces en Cancérologie de Marseille (CEPCM), 264 Boulevard de Saint Pierre, 13005, Marseille

Germany

2 sites · Ended
Universitaetsklinikum Jena KöR
Hematology and internal Oncology, Am Klinikum 1, Lobeda, Jena
Medizinische Hochschule Hannover
Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Carl-Neuberg-Strasse 1, Gross Buchholz, Hanover

Italy

4 sites · Ongoing, recruitment ended
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Ematologia, Via Pietro Albertoni 15, 40138, Bologna
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
DIAGNOSTICA PER IMMAGINI, RADIOTERAPIA ONCOLOGICA ED EMATOLOGIA, Largo Francesco Vito 1, 00168, Rome
ASST Grande Ospedale Metropolitano Niguarda
Ematologia, Piazza Dell'ospedale Maggiore 3, 20162, Milan
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
Ematologia, Via Francesco Sforza 28, 20122, Milan

Netherlands

1 site · Ended
Radboud universitair medisch centrum Stichting
Department of Hematology, Geert Grooteplein Zuid 10, 6525 GA, Nijmegen

Poland

4 sites · Ongoing, recruitment ended
Copernicus Podmiot Leczniczy Sp. z o.o.
Wojewódzkie Centrum Onkologii, Al. Zwyciestwa 31/32, 80-219, Gdansk
Aidport Sp. z o.o.
AIDPORT SPÓŁKA Z OGRANICZONĄ ODPOWIEDZIALNOŚCIĄ, Ul Ksiedza Stanisława Kozierowskiego 24, 60-185, Skorzewo
Uniwersyteckie Centrum Kliniczne
Klinika Hematologii i Transplantologii, Ul. Mariana Smoluchowskiego 17, 80-214, Gdansk
Pratia Hematologia Sp. z o.o.
Pratia Onkologia Katowice, Ul. Tadeusza Kosciuszki 92, 40-519, Katowice

Spain

4 sites · Ongoing, recruitment ended
Institut Catala D'oncologia
Hematology, Avinguda De La Gran Via De L'hospitalet 199-203, 08908, L'hospitalet De Llobregat
Hospital Universitario 12 De Octubre
Hematology, Avenida De Cordoba Sn, 28041, Madrid
Hospital Universitario Regional De Malaga
Hematology and Hemotherapy, Avenida De Carlos De Haya S/N, 29010, Malaga
Hospital Universitario La Paz
Hematology and Hemotherapy, Paseo De La Castellana 261, 28046, Madrid

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2025-03-19
Germany 2025-04-29
Italy 2025-02-20 2025-03-10 2026-03-03
Netherlands 2025-07-31
Poland 2025-01-30 2025-09-30 2026-03-03
Spain 2025-02-07 2025-07-17 2026-03-03

Application history

7 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-09-05 Spain Acceptable
2025-01-15
2025-01-15
2 NON SUBSTANTIAL MODIFICATION NSM-1 2025-01-24 Acceptable
2025-01-15
2025-01-24
3 SUBSTANTIAL MODIFICATION SM-1 2025-02-05 Acceptable 2025-03-17
4 SUBSEQUENT ADDITION OF MSC APP-4 2025-02-11 2025-04-29
5 SUBSTANTIAL MODIFICATION SM-2 2025-02-13 Acceptable 2025-04-30
6 SUBSTANTIAL MODIFICATION SM-3 2025-05-23 Spain Acceptable
2025-08-20
2025-08-20
7 SUBSTANTIAL MODIFICATION SM-4 2025-11-19 Spain Acceptable
2026-01-19
2026-01-19