Personalized extended interval dosing of natalizumab in relapsing remitting multiple sclerosis (NEXT-MS)

2024-513105-31-00 Therapeutic use (Phase IV) Ongoing, recruitment ended

Start 30 Jul 2024 · Status Ongoing, recruitment ended · 1 EU/EEA countries · 17 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic use (Phase IV)
Status Ongoing, recruitment ended
Participants planned 440
Countries 1
Sites 17

Multiple Sclerosis

Our objective is to test feasibility and validate safety of personalized extended interval dosing of natalizumab starting from 6 weeks in a large real-life cohort across the Netherlands.

Key facts

Sponsor
Amsterdam UMC Stichting
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Trial duration
30 Jul 2024 → ongoing
Decision date (initial)
2024-07-30
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

External identifiers

EU CT number
2024-513105-31-00
EudraCT number
2019-002566-13
ClinicalTrials.gov
NCT04225312

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Therapy, Safety, Efficacy

Our objective is to test feasibility and validate safety of personalized extended interval dosing of natalizumab starting from 6 weeks in a large real-life cohort across the Netherlands.

Conditions and MedDRA coding

Multiple Sclerosis

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 4

  1. Diagnosis of relapsing remitting multiple sclerosis according to the 2017 criteria
  2. 6 or more consecutive natalizumab infusions
  3. 18 years or older
  4. Agreed to participate (written informed consent)

Exclusion criteria 2

  1. High titer natalizumab (>100AU/ml) antibodies
  2. Contraindication for yearly magnetic resonance imaging (MRI) (ie, have pacemakers or other contraindicated implanted metal devices, or have claustrophobia that cannot be medically managed)

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Radiological disease activity (new/enlarging T2 lesions on brain MRI) after two years

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 3

Tysabri 300 mg concentrate for solution for infusion

PRD10194542 · Product

Active substance
Natalizumab
Substance synonyms
AN100226M
Pharmaceutical form
SOLUTION FOR INFUSION
Route of administration
INTRAVENOUS INFUSION
Max daily dose
300 mg milligram(s)
Max total dose
300 mg milligram(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
L04AG03 — -
Marketing authorisation
EU/1/06/346/001
MA holder
BIOGEN NETHERLANDS B.V.
MA country
Iceland
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Tyruko 300 mg concentrate for solution for infusion

PRD10854419 · Product

Active substance
Natalizumab
Pharmaceutical form
SOLUTION FOR INFUSION
Route of administration
INTRAVENOUS INFUSION
Max daily dose
300 mg milligram(s)
Max total dose
300 mg milligram(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
L04AA23 — -
Marketing authorisation
EU/1/23/1745/001
MA holder
SANDOZ GMBH
MA country
EU
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Tysabri 150 mg solution for injection in pre-filled syringe

PRD10194555 · Product

Active substance
Natalizumab
Substance synonyms
AN100226M
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
SUBCUTANEOUS INJECTION
Max daily dose
300 mg milligram(s)
Max total dose
300 mg milligram(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
L04AG03 — -
Marketing authorisation
EU/1/06/346/002
MA holder
BIOGEN NETHERLANDS B.V.
MA country
Iceland
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Amsterdam UMC Stichting

Sponsor organisation
Amsterdam UMC Stichting
Address
De Boelelaan 1117
City
Amsterdam
Postcode
1081 HV
Country
Netherlands

Scientific contact point

Organisation
Amsterdam UMC Stichting
Contact name
L.M.Y. Gelissen

Public contact point

Organisation
Amsterdam UMC Stichting
Contact name
L.M.Y. Gelissen

Locations

1 EU/EEA country · 17 investigational sites

By country

CountryMS statusPlanned subjectsSites
Netherlands Ongoing, recruitment ended 440 17
Rest of world 0

Investigational sites

Netherlands

17 sites · Ongoing, recruitment ended
Spaarne Gasthuis Stichting
Neurology, Boerhaavelaan 24, 2035 RC, Haarlem
Jeroen Bosch Ziekenhuis Stichting
Neurology, Henri Dunantstraat 1, 5223 GZ, 'S-Hertogenbosch
Flevoziekenhuis Stichting
Neurology, Hospitaalweg 1, 1315 RA, Almere
Olvg
Neurology, Oosterpark 9, Netherlands, Amsterdam
Reinier de Graaf Groep
Neurology, Reinier De Graafweg 5, 2625 AD, Delft
Alrijne Zorggroep Stichting
Neurology, Simon Smitweg 1, 2353 GA, Leiderdorp
St. Antonius Ziekenhuis
Neurology, Koekoekslaan 1, Netherlands, Nieuwegein
VUmc Stichting
Neurologie, De Boelelaan 1117, 1081 HV, Amsterdam
Rijnstate Ziekenhuis Stichting
Neurology, Wagnerlaan 55, 6815 AD, Arnhem
Amphia Hospital
Neruology, Molengracht 21, 4818 CK, Breda
Maasstad Ziekenhuis Stichting
Neurology, Maasstadweg 21, 3079 DZ, Rotterdam
Isala Klinieken Stichting
Neurology, Dokter Van Heesweg 2, 8025 AB, Zwolle
Slingeland Ziekenhuis
Neurology, Kruisbergseweg 25, 7009 BL, Doetinchem
Ommelander Ziekenhuis Groningen B.V.
Neurology, Pastorieweg 1, 9679 BJ, Scheemda
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Neurology, Dr. Molewaterplein 40, 3015 GD, Rotterdam
Elisabeth-TweeSteden Ziekenhuis
Neurology, Hilvarenbeekse Weg 60, Netherlands, Tilburg
Diakonessenhuis Stichting
Neurology, Bosboomstraat 1, 3582 KE, Utrecht

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Netherlands 2024-07-30 2024-07-30 2024-11-04

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 5 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1_Protocol 2024-513105-31-00 11
Recruitment arrangements (for publication) Recruitment statement 1
Subject information and informed consent form (for publication) L1_ SIS and ICF SUPERNEXT Dutch 9
Summary of Product Characteristics (SmPC) (for publication) G2_ SmPC Tysabri 1
Summary of Product Characteristics (SmPC) (for publication) G2_SmPC Tyruko 1

Application history

2 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-07-22 Netherlands Acceptable with conditions
2024-07-30
2024-07-30
2 SUBSTANTIAL MODIFICATION SM-1 2026-01-05 Netherlands Acceptable with conditions 2026-01-29