Cultured Autologous Oral Mucosa Epithelial sheet for the Treatment of Bilateral Limbal Stem Cell Deficiency FEMJA for « Feuillet Epithélial de Muqueuse Jugale Autologue »

2024-513939-24-00 Protocol 69HCL19_0032 Phase I and Phase II (Integrated) - First administration to humans Ongoing, recruiting

Start 13 Nov 2020 · Status Ongoing, recruiting · 1 EU/EEA countries · 1 sites · Protocol 69HCL19_0032

Overview

Sponsor-declared trial summary

Phase Phase I and Phase II (Integrated) - First administration to humans
Status Ongoing, recruiting
Participants planned 40
Countries 1
Sites 1

Bilateral Limbal Stem Cell Deficiency

Key facts

Sponsor
Hospices Civils De Lyon
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Eye Diseases [C11]
Trial duration
13 Nov 2020 → ongoing
Decision date (initial)
2024-09-19
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

External identifiers

EU CT number
2024-513939-24-00
EudraCT number
2019-003215-63
ClinicalTrials.gov
NCT03949881

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Bilateral Limbal Stem Cell Deficiency

VersionLevelCodeTermSystem organ class
20.1 PT 10072138 Limbal stem cell deficiency 100000004853

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Hospices Civils De Lyon

Sponsor organisation
Hospices Civils De Lyon
Address
3 Quai Des Celestins, Bp 2251 Bp 2251
City
Lyon Cedex 02
Postcode
69229
Country
France

Scientific contact point

Organisation
Hospices Civils De Lyon
Contact name
Pr Carole BURILLON

Public contact point

Organisation
Hospices Civils De Lyon
Contact name
Pr Carole BURILLON

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ongoing, recruiting 40 1
Rest of world 0

Investigational sites

France

1 site · Ongoing, recruiting
Hospices Civils De Lyon
Service d'Ophtalmologie, 5 Place D Arsonval, 69437, Lyon Cedex 03

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2020-11-13 2020-11-13

Application history

4 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-07-31 France Acceptable
2024-08-27
2024-09-19
2 SUBSTANTIAL MODIFICATION SM-1 2024-10-25 France Acceptable
2024-11-18
2024-12-04
3 NON SUBSTANTIAL MODIFICATION NSM-1 2025-04-30 France Acceptable
2024-11-18
2025-04-30
4 SUBSTANTIAL MODIFICATION SM-2 2025-11-03 France Acceptable
2025-12-08
2025-12-09