Study of Safety, Tolerability, Pharmacodynamics and Pharmacokinetics of NIO752 in Early Alzheimer's Disease Participants

2024-514004-14-00 Protocol NIO752B12201 Human pharmacology (Phase I) - Other Ongoing, recruitment ended

Start 23 Feb 2023 · Status Ongoing, recruitment ended · 4 EU/EEA countries · 10 sites · Protocol NIO752B12201

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Ongoing, recruitment ended
Participants planned 37
Countries 4
Sites 10

Alzheimer’s Disease

Key facts

Sponsor
Novartis Pharma AG
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Trial duration
23 Feb 2023 → ongoing
Decision date (initial)
2024-08-02
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

External identifiers

EU CT number
2024-514004-14-00
EudraCT number
2022-000921-26
ClinicalTrials.gov
NCT05469360

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Alzheimer’s Disease

VersionLevelCodeTermSystem organ class
20.0 LLT 10001896 Alzheimer's disease 10029205

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Novartis Pharma AG

Sponsor organisation
Novartis Pharma AG
Address
Lichtstrasse 35
City
Basel
Postcode
4056
Country
Switzerland

Scientific contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Public contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Locations

4 EU/EEA countries · 10 investigational sites

By country

CountryMS statusPlanned subjectsSites
Finland Ended 3 2
France Ongoing, recruitment ended 13 3
Spain Ongoing, recruitment ended 15 3
Sweden Ended 6 2
Rest of world 0

Investigational sites

Finland

2 sites · Ended
Clinical Research Services Turku CRST Oy
1101 : Clinical Research Unit (Phase I), Joukahaisenkatu 2 B, 20520, Turku
University Of Eastern Finland
1102 : Institute of Clinical Medicine, Brain Research Unit, P. O. Box 1627, 70211, Kuopio

France

3 sites · Ongoing, recruitment ended
Assistance Publique Hopitaux De Paris
3001 : département des maladies du système nerveux, 47 Boulevard De L Hopital, 75651, Paris Cedex 13
Centre Hospitalier Universitaire De Lille
3002 : Centre Mémoire de Ressources et de Recherche, Rue Emile Laine, 59037, Lille Cedex
Centre Hospitalier Universitaire De Toulouse
3000 : Département de Neurologie, 1 Place Du Docteur Joseph Baylac, 31300, Toulouse

Spain

3 sites · Ongoing, recruitment ended
Hospital De La Santa Creu I Sant Pau
2000:Neurología, Carrer De San Quinti 89, 08041, Barcelona
Hospital Universitario Dr Peset Aleixandre
2002:Neurología, Avinguda De Gaspar Aguilar 90, 46017, Valencia
Hospital Clinic De Barcelona
2001:Neurología, Calle Villarroel 170, 08036, Barcelona

Sweden

2 sites · Ended
Region Skane Skanes Universitetssjukhus
1202 : Minneskliniken, St. Johns, Fritz Bauers Gata 5, Malmo
Karolinska University Hospital
1201 : ME Åldrande Kognitiv Forskning, Halsovagen, Flemingsberg, Huddinge

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Finland 2023-10-03 2025-08-05 2023-10-03 2023-12-12
France 2023-06-21 2023-06-21 2026-03-12
Spain 2023-09-05 2023-09-05 2026-02-03
Sweden 2023-02-23 2025-07-31 2023-02-23 2023-11-29

Application history

6 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-07-12 Sweden Acceptable with conditions
2024-08-02
2024-08-02
2 NON SUBSTANTIAL MODIFICATION NSM-1 2024-12-04 Sweden Acceptable with conditions
2024-08-02
2024-12-04
3 SUBSTANTIAL MODIFICATION SM-1 2025-03-11 Sweden Acceptable
2025-05-08
2025-05-09
4 NON SUBSTANTIAL MODIFICATION NSM-2 2025-05-27 Acceptable
2025-05-08
2025-05-27
5 SUBSTANTIAL MODIFICATION SM-2 2025-06-06 Sweden Acceptable
2025-08-25
2025-08-27
6 SUBSTANTIAL MODIFICATION SM-3 2025-10-15 Acceptable
2026-01-07
2026-01-09