Novel treatment with botulinum toxin for erectile dysfunction unresponsive to conventional treatment

2024-514518-10-00 Protocol BTXDE Therapeutic exploratory (Phase II) Ongoing, recruiting

Start 31 Oct 2024 · Status Ongoing, recruiting · 1 EU/EEA countries · 2 sites · Protocol BTXDE

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ongoing, recruiting
Participants planned 114
Countries 1
Sites 2

Erectile dysfunction

To test the therapeutic efficacy of intracavernous injections (ICI) of Onabotulinumtoxin A (BoNT-A) in the treatment of erectile dysfunction (ED)

Key facts

Sponsor
Clinica Universidad De Navarra
Participant type
Patients
Age range
18-64 years
Gender
Male
Therapeutic area
Diseases [C] - Male Urogenital Diseases [C12]
Trial duration
31 Oct 2024 → ongoing
Decision date (initial)
2024-09-20
Transition trial
No
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
No
Funding sources
Clínica Universidad de Navarra

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Efficacy

To test the therapeutic efficacy of intracavernous injections (ICI) of Onabotulinumtoxin A (BoNT-A) in the treatment of erectile dysfunction (ED)

Secondary objectives 4

  1. To check the best therapeutic secondary adherence to its six-monthly administration in hospital by comparatively analyzing through the clinical history the patient's preferences between daily or on-demand consumption of oral/intracavernosal mediation vs six-monthly intracavernosal hospital administration.
  2. To rule out the presence of relevant adverse effects derived from this procedure.
  3. To assess the duration of the treatment effect.
  4. To define the profile of candidates for this treatment.

Conditions and MedDRA coding

Erectile dysfunction

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 5

  1. Patients diagnosed with ED with insufficient response to IPDE5 or intracavernous injections with Caverject or Bimix/Trimix (IIEF-15 questionnaire score ≤ 12).
  2. The patient is over 30 years old
  3. The patient, or his or her representative, has given consent to participate in the study.
  4. The patient must, in the opinion of the investigator, be able to comply with all the requirements of the clinical trial.
  5. Patient must commit to attending follow-up appointments and undergoing the appropriate tests.

Exclusion criteria 10

  1. Patients who do not accept informed consent
  2. Patients under 30 years of age.
  3. Known hypersensitivity to BoNT-A
  4. Serious infections or diseases or hepatic, renal or spinal cord failure that discourage the patient's participation in the study, according to the researcher's criteria.
  5. Patients with robotic radical prostatectomy less than 6 months ago
  6. Patients with a history of known neurogenic damage
  7. Patients with a history of radiotherapy treatment
  8. Patients with known psychiatric disorder
  9. Patients with anatomical abnormalities in the penis.
  10. Patients who do not accept or cannot commit to attending the follow-up sessions.

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Subjective perception of rigidity

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

SCP1061961 · ATC

Route of administration
LOCAL INJECTION
Max daily dose
1 ml millilitre(s)
Max total dose
1 ml millilitre(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
M03AX01 — BOTULINUM TOXIN
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Placebo 1

Sodium Chloride Solution 0.9%

SUB20079 · Substance

Active substance
Sodium Chloride Solution 0.9%
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
LOCAL INJECTION
Max daily dose
1 ml millilitre(s)
Max total dose
1 ml millilitre(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
- — -
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Clinica Universidad De Navarra

Sponsor organisation
Clinica Universidad De Navarra
Address
Avenue Pio XII 36
City
Pamplona
Postcode
31008
Country
Spain

Scientific contact point

Organisation
Clinica Universidad De Navarra
Contact name
José Enrique Robles García

Public contact point

Organisation
Clinica Universidad De Navarra
Contact name
José Enrique Robles García

Locations

1 EU/EEA country · 2 investigational sites

By country

CountryMS statusPlanned subjectsSites
Spain Ongoing, recruiting 114 2
Rest of world 0

Investigational sites

Spain

2 sites · Ongoing, recruiting
Clinica Universidad De Navarra
Urología, Avenue Pio XII 36, 31008, Pamplona
Clinica Universidad De Navarra
Urología, Calle Marquesado De Santa Marta 1, 28027, Madrid

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Spain 2024-10-31 2024-11-18

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 5 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Recruitment arrangements (for publication) K1_Recruitment arrangements 1
Recruitment arrangements (for publication) K1_Recruitment arrangements_v2 2
Subject information and informed consent form (for publication) L1_SIS and ICF all subjets 1
Subject information and informed consent form (for publication) L1_SIS and ICF all subjets_reviewed 1.1
Summary of Product Characteristics (SmPC) (for publication) G2_SmPC Botox 1

Application history

3 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-06-14 Spain Acceptable
2024-08-29
2024-09-20
2 NON SUBSTANTIAL MODIFICATION NSM-1 2024-11-06 Spain Acceptable
2024-08-29
2024-11-06
3 SUBSTANTIAL MODIFICATION SM-2 2025-11-25 Spain Acceptable 2025-12-29