Phase 1 Study of Revumenib in Combination with Intensive Chemotherapy in Participants with AML Harboring Alterations in KMT2A/MLL, NPM1, or NUP98 Genes

2024-514531-18-00 Protocol SNDX-5613-0708 Human pharmacology (Phase I) - Other Ongoing, recruiting

Start 20 May 2025 · Status Ongoing, recruiting · 2 EU/EEA countries · 10 sites · Protocol SNDX-5613-0708

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Ongoing, recruiting
Participants planned 76
Countries 2
Sites 10

Acute Myeloid Leukemias

Key facts

Sponsor
Syndax Pharmaceuticals Inc.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
20 May 2025 → ongoing
Decision date (initial)
2025-02-06
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
Yes

External identifiers

EU CT number
2024-514531-18-00
ClinicalTrials.gov
NCT06226571

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Acute Myeloid Leukemias

VersionLevelCodeTermSystem organ class
20.1 LLT 10024330 Leukemia acute 10029104

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Syndax Pharmaceuticals Inc.

Sponsor organisation
Syndax Pharmaceuticals Inc.
Address
730 3rd Avenue Floor 9
City
New York
Postcode
10017-3206
Country
United States

Scientific contact point

Organisation
Syndax Pharmaceuticals Inc.
Contact name
Jessica Clement

Public contact point

Organisation
Syndax Pharmaceuticals Inc.
Contact name
Clinical Trials

Locations

2 EU/EEA countries · 10 investigational sites

By country

CountryMS statusPlanned subjectsSites
Netherlands Ongoing, recruiting 4 1
Spain Ongoing, recruiting 18 9
Rest of world
United States, Australia, United Kingdom, Canada
54

Investigational sites

Netherlands

1 site · Ongoing, recruiting
Universitair Medisch Centrum Utrecht
Hematology, Heidelberglaan 100, 3584 CX, Utrecht

Spain

9 sites · Ongoing, recruiting
Hospital General Universitario Gregorio Maranon
Hematology, Calle Del Doctor Esquerdo 46, 28007, Madrid
Hospital Clinic De Barcelona
Hematolgy, Calle Villarroel 170, 08036, Barcelona
Hospital Universitario De Salamanca
Hematology, Paseo De San Vicente 58-182, 37007, Salamanca
Hospital Universitario Y Politecnico La Fe
Hematology, Avenida Fernando Abril Martorell 106, 46026, Valencia
Hospital Universitario Marques De Valdecilla
Hematology, Avenida Valdecilla Sn, 39008, Santander
Hospital Universitario 12 De Octubre
Hematology, Avenida De Cordoba Sn, 28041, Madrid
University Hospital Virgen Del Rocio S.L.
Hematology, Avenida De Manuel Siurot S/n, 41013, Sevilla
Hospital Universitario Virgen De Las Nieves
Hematology, Avenida De Las Fuerzas Armadas 2, 18014, Granada
Hospital San Pedro De Alcantara
Hematology, Avenida De Pablo Naranjo Porras S/n, 10002, Caceres

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Netherlands 2025-07-02 2025-08-07
Spain 2025-05-20 2025-05-22

Application history

4 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-10-22 Spain Acceptable with conditions
2025-02-03
2025-02-03
2 SUBSTANTIAL MODIFICATION SM-1 2025-03-10 Spain Acceptable
2025-04-28
2025-05-05
3 NON SUBSTANTIAL MODIFICATION NSM-1 2025-05-30 Spain Acceptable
2025-04-28
2025-05-30
4 SUBSTANTIAL MODIFICATION SM-2 2026-01-21 Spain Acceptable
2026-04-24
2026-04-28