A Randomized, Placebo-Controlled, Double-Blind, Single Dose, Phase 1 Study to Explore the PK/PD Relationship of QRL-101 in People Living With ALS

2024-515021-29-00 Protocol QRL-101-04 Human pharmacology (Phase I) - Other Ended

Start 11 Nov 2024 · End 22 Aug 2025 · Status Ended · 1 EU/EEA countries · 1 sites · Protocol QRL-101-04

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Ended
Participants planned 12
Countries 1
Sites 1

Amyotrophic lateral sclerosis (ALS)

Key facts

Sponsor
Quralis Corp.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Trial duration
11 Nov 2024 → 22 Aug 2025
Decision date (initial)
2024-10-14
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Amyotrophic lateral sclerosis (ALS)

VersionLevelCodeTermSystem organ class
21.1 PT 10002026 Amyotrophic lateral sclerosis 100000004852

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Quralis Corp.

Sponsor organisation
Quralis Corp.
Address
35 Cambridge Park Drive
City
Cambridge
Postcode
02140-2325
Country
United States

Scientific contact point

Organisation
Quralis Corp.
Contact name
Doug Williamson, MD

Public contact point

Organisation
Quralis Corp.
Contact name
Principal Investigator Prof. dr. Leonard van den Berg

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Netherlands Ended 12 1
Rest of world 0

Investigational sites

Netherlands

1 site · Ended
Universitair Medisch Centrum Utrecht
ALS Centrum, Divisie Hersenen, Heidelberglaan 100, 3584 CX, Utrecht

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Netherlands 2024-11-11 2025-08-22 2024-11-11 2025-07-22

Application history

7 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-07-08 Netherlands Acceptable with conditions
2024-10-07
2024-10-14
2 NON SUBSTANTIAL MODIFICATION NSM-1 2024-10-21 Netherlands Acceptable with conditions
2024-10-07
2024-10-21
3 NON SUBSTANTIAL MODIFICATION NSM-2 2024-10-24 Netherlands Acceptable with conditions
2024-10-07
2024-10-24
4 NON SUBSTANTIAL MODIFICATION NSM-3 2024-10-29 Netherlands Acceptable with conditions
2024-10-07
2024-10-29
5 SUBSTANTIAL MODIFICATION SM-1 2024-11-15 Netherlands Acceptable
2025-02-17
2025-02-20
6 NON SUBSTANTIAL MODIFICATION NSM-4 2025-03-21 Netherlands Acceptable
2025-02-17
2025-03-21
7 SUBSTANTIAL MODIFICATION SM-3 2025-03-24 Netherlands Acceptable 2025-05-01