Single-blind randomized clinical trial in premature infants with Respiratory Distress Syndrome (RDS) eligible for treatment with exogenous surfactant identified early by lung ultrasonography.

2024-515641-42-00 Therapeutic exploratory (Phase II) Ongoing, recruiting

Start 26 Jun 2024 · Status Ongoing, recruiting · 1 EU/EEA countries · 1 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ongoing, recruiting
Participants planned 30
Countries 1
Sites 1

Premature infants with Respiratory Distress Syndrome (RDS)

Compare the efficacy of two administration schemes of exogenous pulmonary surfactant in preterm newborns with Respiratory Distress Syndrome (one indicated based on lung ultrasound criteria versus the other following current guideline recommendations) in terms of reducing the number of intubations in the first 72 hours …

Key facts

Sponsor
Fundacio Institut De Recerca De L'Hospital De La Santa Creu I Sant Pau
Participant type
Pediatric, Patients
Age range
0-17 years
Gender
Male and Female
Therapeutic area
Diseases [C] - Respiratory Tract Diseases [C08]
Trial duration
26 Jun 2024 → ongoing
Decision date (initial)
2024-06-26
Transition trial
Yes
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
Yes

External identifiers

EU CT number
2024-515641-42-00
EudraCT number
2022-003106-72

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Efficacy

Compare the efficacy of two administration schemes of exogenous pulmonary surfactant in preterm newborns with Respiratory Distress Syndrome (one indicated based on lung ultrasound criteria versus the other following current guideline recommendations) in terms of reducing the number of intubations in the first 72 hours of life.

Conditions and MedDRA coding

Premature infants with Respiratory Distress Syndrome (RDS)

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 1

  1. Premature newborns of both sexes, between 24 and 32 weeks and/or ≤ 1500 grams at birth, who do not meet any of the exclusion criteria, will be included.

Exclusion criteria 6

  1. Lack of parental informed consent.
  2. Patients presenting with any of the following conditions: • Chromosomal abnormalities or complex congenital malformations.
  3. Patients presenting with any of the following conditions: Congenital lung diseases.
  4. Patients presenting with any of the following conditions: Severe sepsis or septic shock.
  5. Patients presenting with any of the following conditions: Meconium aspiration syndrome.
  6. Patients presenting with any of the following conditions: Administration of surfactant in the delivery room.

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Intubation rate in the next 72 hours of life.

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Curosurf, 240 mg/3 ml, suspensão para instilação endotraqueobrônquica

PRD11035751 · Product

Active substance
Phospholipid Fraction, Porcine Lung
Substance synonyms
PHOSPHOLIPID FRACTION FROM PIG LUNG
Pharmaceutical form
ENDOTRACHEOPULMONARY INSTILLATION, SUSPENSION
Route of administration
ENDOTRACHEOPULMONARY USE
Max daily dose
300 mg/kg milligram(s)/kilogram
Max total dose
300 mg/kg milligram(s)/kilogram
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
R07AA02 — NATURAL PHOSPHOLIPIDS
Marketing authorisation
2139988
MA holder
CHIESI FARMACEUTICI S.P.A.
MA country
Portugal
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Fundacio Institut De Recerca De L'Hospital De La Santa Creu I Sant Pau

Sponsor organisation
Fundacio Institut De Recerca De L'Hospital De La Santa Creu I Sant Pau
Address
Calle Sant Quinti 77-79
City
Barcelona
Postcode
08041
Country
Spain

Scientific contact point

Organisation
Fundacio Institut De Recerca De L'Hospital De La Santa Creu I Sant Pau
Contact name
UICEC Sant Pau

Public contact point

Organisation
Fundacio Institut De Recerca De L'Hospital De La Santa Creu I Sant Pau
Contact name
UICEC Sant Pau

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Spain Ongoing, recruiting 30 1
Rest of world 0

Investigational sites

Spain

1 site · Ongoing, recruiting
Hospital De La Santa Creu I Sant Pau
Pediatrics, Calle De San Antonio Maria Claret 167, 08025, Barcelona

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Spain 2024-06-26 2024-06-26

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 4 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1_Protocolo 2022-003106-72_for publication 3
Recruitment arrangements (for publication) K1_Recruitment arrangements 1
Subject information and informed consent form (for publication) L1_SIS and ICF parents 2
Synopsis of the protocol (for publication) D1_Protocolo synopsis_NL 2022-003106-72_for publication 3

Application history

2 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-06-21 Spain Acceptable
2024-06-26
2024-06-26
2 NON SUBSTANTIAL MODIFICATION NSM-1 2025-10-16 Spain Acceptable
2024-06-26
2025-10-16