MRI of Neurometabolic Impairment in ALS and TIA Using Hyperpolarized Pyruvate

2024-516954-24-00 Therapeutic exploratory (Phase II) Ongoing, recruiting

Start 1 May 2020 · Status Ongoing, recruiting · 1 EU/EEA countries · 1 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ongoing, recruiting
Participants planned 46
Countries 1
Sites 1

ALS (Amyotrophic Lateral Sclerosis)

This project seeks to detect and characterize metabolic impairment in patients with Amyotrophic Lateral Sclerosis and patients with Transient Ischemic attack with a new MRI technique termed Hyperpolarized Pyruvate MRI

Key facts

Sponsor
Aarhus Universitet
Participant type
Patients, Healthy volunteers
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Analytical, Diagnostic and Therapeutic Techniques and Equipment [E] - Investigative Techniques [E05]
Trial duration
1 May 2020 → ongoing
Decision date (initial)
2024-09-12
Transition trial
Yes
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

External identifiers

EU CT number
2024-516954-24-00
EudraCT number
2020-000352-36

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Diagnosis

This project seeks to detect and characterize metabolic impairment in patients with Amyotrophic Lateral Sclerosis and patients with Transient Ischemic attack with a new MRI technique termed Hyperpolarized Pyruvate MRI

Conditions and MedDRA coding

ALS (Amyotrophic Lateral Sclerosis)

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 1

  1. All participants: 1) Age 18-85 years. 2) Pre-menopausal women must be confirmed non-pregnant by an onsite test. ALS group: 1) Fulfilling the 2021 Gold Coast criteria. 2) Upper motor neuron symptoms. TIA-group: 1) TIA within the last 10 days. 2) Symptoms must include unilateral weakness of limb or face. 3) Duration af symptoms minimum 10 minutes

Exclusion criteria 1

  1. Contraindications for MRI with contrast: Chronic kidney disease,- Significant cardiac disease such as severe left ventricular outflow obstruction, -Significant obstructive lung disease or severe asthma,- Pacemaker, neurostimulator or cholera implant,- Metal foreign bodies such as fragments and irremovable piercings,- Unsafe medical implants (safety of heart valves, hips and the like must be confirmed),- Intracranial clips or coils,- Claustrophobia,- Largest circumference including arms > 160 cm. Competing neurological, psychiatric, liver or systemic disease including diabetes (except prior TIA, unspecific brain MRI findings, hypertension, atherosclerosis and hyperlipidemia/cholesterolemia which are allowed). Allergy to pyruvate.

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Cerebral metabolism as assesed with 13C label exchange from hyperpolarized pyruvate to bicarbonate, lactate and alanine

Secondary endpoints 1

  1. Disease characterization from clinical exsamination, interviews and patient records.

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Hyperpolarized [1-13C]pyruvate

PRD10284730 · Product

Active substance
Pyruvic Acid
Pharmaceutical form
INJECTION
Route of administration
INTRAVENOUS BOLUS INJECTION/IV INFUSION
Max daily dose
18.92 mg/kg milligram(s)/kilogram
Max total dose
18.92 mg/kg milligram(s)/kilogram
Max treatment duration
1 Day(s)
Authorisation status
Not Authorised
MA holder
AARHUS UNIVERSITY
Paediatric formulation
No
Orphan designation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Aarhus Universitet

Sponsor organisation
Aarhus Universitet
Address
Palle Juul-Jensens Boulevard 82
City
Aarhus N
Postcode
8200
Country
Denmark

Scientific contact point

Organisation
Aarhus Universitet
Contact name
MR Research Centre Aarhus University

Public contact point

Organisation
Aarhus Universitet
Contact name
MR Research Centre Aarhus University

Third parties 1

OrganisationCity, countryDuties
Aarhus Universitet
ORG-100028380
Aarhus N, Denmark On site monitoring

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Denmark Ongoing, recruiting 46 1
Rest of world 0

Investigational sites

Denmark

1 site · Ongoing, recruiting
Aarhus Universitet
Dept.of Neurology, Palle Juul-Jensens Boulevard 82, 8200, Aarhus N

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Denmark 2020-05-01 2020-10-08

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 7 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1_Protocol_EU CT Number 2024-516954-24-00 1.1
Recruitment arrangements (for publication) K1_Recruitment arrangements_placeholder document 1
Subject information and informed consent form (for publication) L1_ICF 1
Subject information and informed consent form (for publication) L1_SIS_ALS 1
Subject information and informed consent form (for publication) L1_SIS_TIA 1
Summary of Product Characteristics (SmPC) (for publication) Blank_reference for SmPC 1.0
Synopsis of the protocol (for publication) D1_Protocol synopsis_DK EU CT Number 2024-516954-24-00 1.0

Application history

3 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-08-15 Denmark Acceptable
2024-09-12
2024-09-12
2 NON SUBSTANTIAL MODIFICATION NSM-1 2024-11-22 Denmark Acceptable
2024-09-12
2024-11-22
3 SUBSTANTIAL MODIFICATION SM-2 2025-01-12 Denmark Acceptable
2025-01-17
2025-01-17