12-month study of probiotic effects in non-infectious uveitis treatment

2024-517946-32-00 Protocol VFN-MIU-2021-01 Therapeutic exploratory (Phase II) Ongoing, recruiting

Start 2 Jun 2023 · Status Ongoing, recruiting · 1 EU/EEA countries · 1 sites · Protocol VFN-MIU-2021-01

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ongoing, recruiting
Participants planned 9
Countries 1
Sites 1

Non-infectious uveitis

To evaluate the efficacy of Escherichia coli Nissle 1917 (ECN) in patients with autoimmune uveitis

Key facts

Sponsor
Vseobecna Fakultni Nemocnice V Praze
Participant type
Patients
Age range
18-64 years
Gender
Male and Female
Therapeutic area
Diseases [C] - Immune System Diseases [C20], Diseases [C] - Eye Diseases [C11]
Trial duration
2 Jun 2023 → ongoing
Decision date (initial)
2024-12-09
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No
Funding sources
Czech Health Research Council (AZV MZ ČR NU23-05-00133)

External identifiers

EU CT number
2024-517946-32-00
EudraCT number
2021-002850-96

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Therapy

To evaluate the efficacy of Escherichia coli Nissle 1917 (ECN) in patients with autoimmune uveitis

Secondary objectives 4

  1. To assess changes in best-corrected visual acuity (BCVA)
  2. To evaluate uveitis activity using SUN criteria
  3. To assess changes in optical coherence tomography (OCT) parameters
  4. To verify the safety and tolerability of ECN

Conditions and MedDRA coding

Non-infectious uveitis

VersionLevelCodeTermSystem organ class
20.0 PT 10075690 Autoimmune uveitis 100000004853

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 1

  1. Principal inclusion criteria: Adults ≥ 18 and < 65 years of age with autoimmune anterior, intermediate, posterior or pan-uveitis, who experienced flare-up of uveitis within 6 months prior to baseline visit

Exclusion criteria 1

  1. Principal exclusion criteria: Uveitis of infectious etiology, active uveitis requiring an increase in systemic therapy or initiation of biological treatment, etc. (See study protocol for full list)

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Time to first disease relapse from the baseline visit (V2)

Secondary endpoints 4

  1. Severity of first relapse according to the SUN system
  2. Total number of relapses during the study
  3. Changes in BCVA
  4. Changes in OCT parameters

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Mutaflor

PRD4943542 · Product

Active substance
Escherichia Coli Strain Nissle 1917
Pharmaceutical form
GASTRO-RESISTANT CAPSULE, HARD
Route of administration
ORAL
Max daily dose
4 billion CFU billion colony forming units
Max total dose
4 billion CFU billion colony forming units
Max treatment duration
12 Month(s)
Authorisation status
Authorised
ATC code
A07FA — ANTIDIARRHEAL MICROORGANISMS
Marketing authorisation
49/442/00-C
MA holder
ARDEYPHARM GMBH
MA country
Czech Republic
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Vseobecna Fakultni Nemocnice V Praze

2 Total trials 2 Recruiting
Academic / Non-commercial
Sponsor organisation
Vseobecna Fakultni Nemocnice V Praze
Address
U Nemocnice 499/2, Nove Mesto Nove Mesto
City
Prague
Postcode
128 00
Country
Czechia

Scientific contact point

Organisation
Vseobecna Fakultni Nemocnice V Praze
Contact name
Prof. MUDr. Jarmila Heissigerová, Ph.D., MBA

Public contact point

Organisation
Vseobecna Fakultni Nemocnice V Praze
Contact name
Mgr. Martina Racková, MBA

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Czechia Ongoing, recruiting 9 1
Rest of world 0

Investigational sites

Czechia

1 site · Ongoing, recruiting
Vseobecna Fakultni Nemocnice V Praze
Dept. of Ophthalmology, U Nemocnice 499/2, Nove Mesto, Prague

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Czechia 2023-06-02 2023-06-09

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 6 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) Study Protocol_VFN-MIU-2021-01_v3_25April2022_clean 3
Protocol (for publication) VFN-MIU-2021-01_Protocol_Amendment_01_Signed 1
Recruitment arrangements (for publication) 1_Nabor_a_inf_souhlas 1
Subject information and informed consent form (for publication) Inform souhlas_VFN-MIU-2021-01_v3_25-4-2022_clean 3
Summary of Product Characteristics (SmPC) (for publication) Mutaflor_SmPC_Summary_of_Product_Characteristics_ 1
Synopsis of the protocol (for publication) Synopsis_Protocol VFN-MIU-2021-01_ver3_25April2022 3

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-10-11 Czechia Acceptable
2024-10-23
2024-12-09