A Phase I, First In Human, open-label study of escalating doses of INA03 administered intravenously as single agent in adult patients with relapse/refractory Acute Leukemia

2024-518265-10-01 Human pharmacology (Phase I) - First administration to humans Ended

Start 3 Jun 2020 · End 24 Feb 2025 · Status Ended · 1 EU/EEA countries · 3 sites

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ended
Participants planned 24
Countries 1
Sites 3

Relapse/ refractory acute Leukemia

Key facts

Sponsor
Institut Paoli Calmettes
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04], Diseases [C] - Immune System Diseases [C20]
Trial duration
3 Jun 2020 → 24 Feb 2025
Decision date (initial)
2024-12-04
Transition trial
Yes
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

External identifiers

EU CT number
2024-518265-10-01
EudraCT number
2019-000814-13
WHO UTN
U1111-1313-4894
ClinicalTrials.gov
NCT03957915

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Relapse/ refractory acute Leukemia

VersionLevelCodeTermSystem organ class
20.0 PT 10059034 Acute myeloid leukaemia recurrent 100000004864
21.1 PT 10067399 Acute biphenotypic leukaemia 100000004864
21.1 LLT 10081514 Acute myeloid leukemia refractory 10029104
20.1 PT 10063620 Acute lymphocytic leukaemia recurrent 100000004864
20.0 PT 10076866 Acute lymphocytic leukaemia refractory 100000004864

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Institut Paoli Calmettes

Sponsor organisation
Institut Paoli Calmettes
Address
232 Boulevard De Sainte Marguerite, Bp 156 Bp 156
City
Marseille
Postcode
13009
Country
France

Scientific contact point

Organisation
Institut Paoli Calmettes
Contact name
Pr VEY Norbert

Public contact point

Organisation
Institut Paoli Calmettes
Contact name
Marina LAROSA

Locations

1 EU/EEA country · 3 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ended 24 3
Rest of world 0

Investigational sites

France

3 sites · Ended
Oncopole Claudius Regaud
Hématologie, 1 Avenue Irene Joliot Curie, 31100, Toulouse
Institut Paoli Calmettes
Unités d'hématologie 2 et évaluation thérapeutique en Oncologie/hématologie, 232 Boulevard De Sainte Marguerite, Bp 156, Marseille
CHU de Bordeaux - Hôpital Haut-Lévêque
Hématologie clinique, 2 Avenue de Magellan, Centre Médico-Chirurgical Magellan, Pessac

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2020-06-03 2025-02-24

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-11-05 France Acceptable
2024-11-27
2024-12-04