Randomized controlled trial comparing immediate versus extended release tacrolimus; reducing calcineurin inhibitor related toxicity in lung transplantation patients

2024-518639-12-00 Therapeutic confirmatory (Phase III) Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 1 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic confirmatory (Phase III)
Status Authorised, recruitment pending
Participants planned 140
Countries 1
Sites 1

lung transplantation

To compare absolute difference in renal function expressed as absolute difference in eGFR, at 2 years compared to baseline, calculated by the 2012 CKD-EPI creatinine–cystatin C equation in patients treated with IR or LCP tacrolimus.

Key facts

Sponsor
Universitair Medisch Centrum Groningen
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Respiratory Tract Diseases [C08]
Decision date (initial)
2025-01-28
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

External identifiers

EU CT number
2024-518639-12-00
EudraCT number
2020-000760-36

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Therapy, Efficacy

To compare absolute difference in renal function expressed as absolute difference in eGFR,
at 2 years compared to baseline, calculated by the 2012 CKD-EPI creatinine–cystatin C
equation in patients treated with IR or LCP tacrolimus.

Secondary objectives 1

  1. The key secondary objective is graft function. Other secondary endpoints are changes in known side effects of calcineurin inhibitors i.e. hypertension, new onset diabetes mellitus and neurotoxicity.

Conditions and MedDRA coding

lung transplantation

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 1

  1. For both the de novo and conversion study: - Single or bilateral lung transplantation - Age > 18 years - On twice daily tacrolimus with stable trough levels in target range - Written informed consent - Participant in the TransplantLines biobank study in the UMCG Additional criteria for: - De novo study: De novo lung transplant patients are recruited before transplantation, and subsequently in all patients put on tacrolimus intravenously. Participants can be randomized when they are on stable daily dosage. - Conversion study: o At least one year after lung transplantation with a stable clinical course and lung function o eGFR >30ml/min*1.73m2 calculated with the CKD-EPI formula

Exclusion criteria 1

  1. Administration of mTOR inhibitors; everolimus, sirolimus - Quadruple immunosuppression - Renal transplantation - The subject has any disease or condition that might interfere with completion of this study or reaching the primary endpoint (e.g., life expectancy of <3 years, renal replacement therapy at start study

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Kidney function

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Envarsus 0.75 mg prolonged-release tablets

PRD11085939 · Product

Active substance
Tacrolimus
Pharmaceutical form
PROLONGED-RELEASE TABLET
Route of administration
ORAL
Max daily dose
10 mg milligram(s)
Max total dose
10 mg milligram(s)
Max treatment duration
24 Month(s)
Authorisation status
Authorised
ATC code
L04AD02 — -
Marketing authorisation
PLGB 08829/0183
MA holder
CHIESI LIMITED
MA country
United Kingdom
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Comparator 1

PROGRAF 1 mg capsule

PRD10226711 · Product

Active substance
Tacrolimus
Substance synonyms
TACROLIMUS ANHYDROUS
Pharmaceutical form
CAPSULE, HARD
Route of administration
ORAL
Max daily dose
10 mg milligram(s)
Max total dose
10 mg milligram(s)
Max treatment duration
24 Month(s)
Authorisation status
Authorised
ATC code
L04AD02 — -
Marketing authorisation
8912/2016/02
MA holder
ASTELLAS PHARMA EUROPE B.V.
MA country
Romania
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Universitair Medisch Centrum Groningen

Sponsor organisation
Universitair Medisch Centrum Groningen
Address
Hanzeplein 1
City
Groningen
Postcode
9713 GZ
Country
Netherlands

Scientific contact point

Organisation
Universitair Medisch Centrum Groningen
Contact name
C.T.Gan

Public contact point

Organisation
Universitair Medisch Centrum Groningen
Contact name
C.T.Gan

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Netherlands Authorised, recruitment pending 140 1
Rest of world 0

Investigational sites

Netherlands

1 site · Authorised, recruitment pending
University Medical Center Groningen
Respiratory disease, tuberculosis and lung transplantation, Hanzeplein 1, 9713 GZ, Groningen

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 5 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1 Protocol 20245186391200 5
Recruitment arrangements (for publication) Blanc document 1
Subject information and informed consent form (for publication) L1 SIS and ICF 2024-518639-12-00 3
Summary of Product Characteristics (SmPC) (for publication) E2 SmPC Envarsus 1
Summary of Product Characteristics (SmPC) (for publication) E2 SmPC Prograft 1

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2025-01-27 Netherlands Acceptable
2025-01-28
2025-01-28