Role in GVHD prophylaxis of Vitamin D in patients undergoing allogeneic transplantation of stem cells. Phase II Pilot Study

2024-518738-97-00 Protocol D AGAINST GVH Therapeutic exploratory (Phase II) Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 1 sites · Protocol D AGAINST GVH

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Authorised, recruitment pending
Participants planned 20
Countries 1
Sites 1

haematologic condition who need staminal cells transplant

Evaluation of the effectiveness of vitamin D on the degree si severity of acute and chronic GvHD

Key facts

Sponsor
Azienda Ospedaliero Universitaria Pisana
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Hemic and Lymphatic Diseases [C15]
Decision date (initial)
2024-11-19
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No
Funding sources
S.P.A: Società Prodotti Antibiotici

External identifiers

EU CT number
2024-518738-97-00
EudraCT number
2020-003994-23

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Efficacy

Evaluation of the effectiveness of vitamin D on the degree si severity of acute and chronic GvHD

Secondary objectives 1

  1. - Assessment of variation in circulating lymphocyte subpopulations on peripheral blood - Assessment of vitamin D receptor surface expression (VDR) and modulation in response to vitamin D treatment on lymphocyte subpopulations. - Evaluation of any adverse events brought about by cholecalciferol intake.

Conditions and MedDRA coding

haematologic condition who need staminal cells transplant

VersionLevelCodeTermSystem organ class
20.0 LLT 10019426 Hematologic disorder 10005329

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 1

  1. - Patients aged > 18 years. Male and female - Diagnosis of any oncohematologic disease with transplant indication, also allowed patients not in clinical response - Patients undergoing allogeneic stem cell transplantation regardless of conditioning regimen and HSC source - Ability to sign informed consent

Exclusion criteria 1

  1. - Transplantation from T-depleted or T-selected product; - Documented intolerance to the drug or any of its excipients; - Ongoing vitamin D therapy for any medical condition; -Hypercalcemia, hypercalciuria, kidney stones, renal failure; - Age < 18 years - Subjects who are not deemed legally capable of consent. - In the case of female: sex pregnancy and/or lactation.

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Reducing the severity of GVHD

Secondary endpoints 1

  1. - Evaluation of circulating lymphocyte subpopulations on peripheral blood - Assessment of vitamin D receptor (VDR) surface expression and modulation in response to vitamin D treatment on lymphocyte subpopulations. - Evaluation of the soluble fraction of VDR on serum - post hoc evaluation of the role of polymorphisms (SNPs) of recipient and donor VDR on response to vitamin D therapy - collection of any adverse events brought about by cholecalciferol intake

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

TREDIMIN 25.000 U.I. /2,5 ml soluzione orale

PRD7966153 · Product

Active substance
Colecalciferol
Pharmaceutical form
ORAL SOLUTION
Route of administration
ORAL USE
Max daily dose
5000 IU/mg international unit(s)/milligram
Max total dose
525000 IU/mg international unit(s)/milligram
Max treatment duration
105 Day(s)
Authorisation status
Authorised
ATC code
A11CC05 — COLECALCIFEROL
Marketing authorisation
042753032
MA holder
SPA – SOCIETÀ PRODOTTI ANTIBIOTICI S.P.A.
MA country
Italy
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Azienda Ospedaliero Universitaria Pisana

6 Total trials 1 Recruiting
Academic / Non-commercial
Sponsor organisation
Azienda Ospedaliero Universitaria Pisana
Address
Via Roma 67
City
Pisa
Postcode
56126
Country
Italy

Scientific contact point

Organisation
Azienda Ospedaliero Universitaria Pisana
Contact name
Clinical Trial Center

Public contact point

Organisation
Azienda Ospedaliero Universitaria Pisana
Contact name
Clinical Trial Center

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Italy Authorised, recruitment pending 20 1
Rest of world 0

Investigational sites

Italy

1 site · Authorised, recruitment pending
Azienda Ospedaliero Universitaria Pisana
U.O. Ematologia, Via Roma 67, 56126, Pisa

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 4 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) Prot Vit D 2024-518738-97-00 4
Recruitment arrangements (for publication) Document not required under the CT Directive 2001 1
Subject information and informed consent form (for publication) TI consenso vit D v4 09102024 4
Summary of Product Characteristics (SmPC) (for publication) Document not submitted under the CT Directive 2001_20_EC 00

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-10-16 Italy Acceptable
2024-11-11
2024-11-19