Phase 1 trial of LAVA-1266, a CD123-targeting bispecific Vγ9Vδ2-T cell engager, in patients with CD123 positive relapsed/refractory (R/R) acute myeloid leukemia (AML) and intermediate risk, high risk, or extremely high-risk myelodysplastic syndrome (MDS)

2024-518831-12-00 Protocol LAVA1266-001 Human pharmacology (Phase I) - First administration to humans Ended

Start 15 Apr 2025 · End 5 Aug 2025 · Status Ended · 1 EU/EEA countries · 5 sites · Protocol LAVA1266-001

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ended
Participants planned 50
Countries 1
Sites 5

CD123 positive R/R AML and intermediate risk, high risk, or extremely high risk MDS.

Key facts

Sponsor
LAVA Therapeutics N.V.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
15 Apr 2025 → 5 Aug 2025
Decision date (initial)
2025-03-19
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

CD123 positive R/R AML and intermediate risk, high risk, or extremely high risk MDS.

VersionLevelCodeTermSystem organ class
27.0 PT 10028533 Myelodysplastic syndrome 100000004864
21.1 PT 10000880 Acute myeloid leukaemia 100000004864

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

LAVA Therapeutics N.V.

Sponsor organisation
LAVA Therapeutics N.V.
Address
Yalelaan 62
City
Utrecht
Postcode
3584 CM
Country
Netherlands

Scientific contact point

Organisation
LAVA Therapeutics N.V.
Contact name
Clinical Trials administrator

Public contact point

Organisation
LAVA Therapeutics N.V.
Contact name
Clinical Trials administrator

Locations

1 EU/EEA country · 5 investigational sites

By country

CountryMS statusPlanned subjectsSites
Spain Ended 20 5
Rest of world
Australia
30

Investigational sites

Spain

5 sites · Ended
Hospital Universitari Vall D Hebron
Hematology, Passeig De La Vall D'Hebron 119-129, 08035, Barcelona
University Hospital Virgen Del Rocio S.L.
Hematology, Avenida De Manuel Siurot S/n, 41013, Sevilla
Clinica Universidad De Navarra
Hematology, Pio XII Etorbidea 36, 31008, Pamplona
Hospital Universitario Y Politecnico La Fe
Hematology, Avenida Fernando Abril Martorell 106, 46026, Valencia
Hospital Universitario De Salamanca
Hematology, Paseo De San Vicente 58-182, 37007, Salamanca

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Spain 2025-04-15 2025-04-25

Application history

2 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-11-29 Spain Acceptable
2025-03-14
2025-03-19
2 NON SUBSTANTIAL MODIFICATION NSM-1 2025-04-02 Spain Acceptable
2025-03-14
2025-04-02