A phase Ib, open-label, ascending dose study to assess safety, tolerability and pharmacokinetics of PIT565 in participants with rheumatoid arthritis (RA)

2024-520196-27-00 Protocol CPIT565C12101 Human pharmacology (Phase I) - Other Authorised, recruiting

Start 1 Oct 2025 · Status Authorised, recruiting · 7 EU/EEA countries · 13 sites · Protocol CPIT565C12101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Authorised, recruiting
Participants planned 57
Countries 7
Sites 13

Rheumatoid Arthritis

Key facts

Sponsor
Novartis Pharma AG
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Immune System Diseases [C20]
Trial duration
1 Oct 2025 → ongoing
Decision date (initial)
2025-07-25
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Rheumatoid Arthritis

VersionLevelCodeTermSystem organ class
23.1 PT 10039073 Rheumatoid arthritis 100000004859

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Novartis Pharma AG

Sponsor organisation
Novartis Pharma AG
Address
Lichtstrasse 35
City
Basel
Postcode
4056
Country
Switzerland

Scientific contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Public contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Locations

7 EU/EEA countries · 13 investigational sites

By country

CountryMS statusPlanned subjectsSites
Bulgaria Ongoing, recruiting 3 1
France Authorised, recruitment pending 5 3
Germany Ongoing, recruiting 4 2
Hungary Authorised, recruitment pending 6 2
Netherlands Authorised, recruitment pending 8 1
Romania Ongoing, recruiting 10 2
Spain Ongoing, recruiting 4 2
Rest of world
Argentina, United Kingdom, China
17

Investigational sites

Bulgaria

1 site · Ongoing, recruiting
Multispecialty hospital for active treatment Sveta Sofia EOOD
1101: Department of Internal Diseases, Bulevard Bilgariya 104, 1404, Sofiya

France

3 sites · Authorised, recruitment pending
Bicetre Hospital
2001:Rheumatology, 78 Rue Du General Leclerc, 94275, Le Kremlin Bicetre Cedex
Centre Hospitalier Regional Et Universitaire De Brest
2002:Rheumatology, Boulevard Tanguy Prigent, 29200, Brest
Assistance Publique Hopitaux De Paris
2003:Rheumatology, 27 Rue Du Faubourg Saint Jacques, 75014, Paris

Germany

2 sites · Ongoing, recruiting
Universitaetsklinikum Jena KöR
1001:Klinik für Innere Medizin III, Rheumatologie/Osteologie, Am Klinikum 1, Lobeda, Jena
Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz KöR
1002:I. Medizinische Klinik und Poliklinik, Langenbeckstrasse 1, Oberstadt, Mainz

Hungary

2 sites · Authorised, recruitment pending
Betegapolo Irgalmasrend Budai Irgalmasrendi Korhaz
50002:Phase I unit, Frankel Leo Ut 17-19, 1027, Budapest II
University Of Szeged
5001 : Phase I unit, Koranyi Fasor 6, 6720, Szeged

Netherlands

1 site · Authorised, recruitment pending
Centre for Human Drug Research
9001: Internal Medicine, Zernikedreef 8, 2333 CL, Leiden

Romania

2 sites · Ongoing, recruiting
Spitalul Clinic Judetean De Urgenta Cluj
6002: Rheumatology, Strada Clinicilor 3-5, 400006, Cluj-Napoca
Arensia Clinics S.R.L.
6001: Internal Medicin, Intrarea Tudor Stefan 38-40, 011658, Bucharest

Spain

2 sites · Ongoing, recruiting
Complexo Hospitalario Universitario De Santiago
8001:Rheumatology, Calle Choupana Da S/n, 15706, Santiago De Compostela
Hospital Universitari Vall D Hebron
8002:Rheumatology, Passeig De La Vall D'Hebron 119-129, 08035, Barcelona

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Bulgaria 2025-10-02 2025-10-02
Germany 2025-10-01 2025-10-01
Romania 2026-04-03 2026-04-03
Spain 2025-10-06 2025-10-06

Application history

4 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2025-03-27 Germany Acceptable
2025-07-21
2025-07-22
2 NON SUBSTANTIAL MODIFICATION NSM-1 2025-08-07 Germany Acceptable
2025-07-21
2025-08-07
3 SUBSTANTIAL MODIFICATION SM-1 2025-10-10 Germany Acceptable
2026-01-19
2026-01-19
4 NON SUBSTANTIAL MODIFICATION NSM-2 2026-04-01 Acceptable
2026-01-19
2026-04-01