First in human, Phase 1a/1b Study of KM-023 in healthy volunteers and Olmsted syndrome patients

2025-521446-20-00 Protocol KM023-101 Human pharmacology (Phase I) - First administration to humans Ongoing, recruiting

Start 27 Jun 2025 · Status Ongoing, recruiting · 1 EU/EEA countries · 2 sites · Protocol KM023-101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ongoing, recruiting
Participants planned 67
Countries 1
Sites 2

Olmsted syndrome

Key facts

Sponsor
Kamari Pharma Ltd.
Participant type
Healthy volunteers, Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Skin and Connective Tissue Diseases [C17]
Trial duration
27 Jun 2025 → ongoing
Decision date (initial)
2025-06-25
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Olmsted syndrome

VersionLevelCodeTermSystem organ class
27.0 PT 10068842 Olmsted syndrome 100000004850

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Kamari Pharma Ltd.

Sponsor organisation
Kamari Pharma Ltd.
Address
Science Park, 3, Pinkhas Sapir 3, Pinkhas Sapir
City
Nes Tsiyona
Postcode
7403626
Country
Israel

Scientific contact point

Organisation
Kamari Pharma Ltd.
Contact name
Liora Braiman

Public contact point

Organisation
Kamari Pharma Ltd.
Contact name
Liora Braiman

Locations

1 EU/EEA country · 2 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ongoing, recruiting 64 2
Rest of world
United Kingdom
3

Investigational sites

France

2 sites · Ongoing, recruiting
Hopital Necker Enfants Malades
Service de dermatologie, 149 Rue De Sevres, 75015, Paris
Biotrial
Unité Clinique, 7 Rue Jean Louis Bertrand, 35000, Rennes

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2025-06-27 2025-06-30

Application history

4 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2025-03-27 France Acceptable with conditions
2025-06-25
2025-06-25
2 NON SUBSTANTIAL MODIFICATION NSM-1 2025-09-26 France Acceptable with conditions
2025-06-25
2025-09-26
3 SUBSTANTIAL MODIFICATION SM-1 2026-01-08 France Acceptable
2026-03-20
2026-03-20
4 SUBSTANTIAL MODIFICATION SM-2 2026-03-23 France Acceptable 2026-04-02