A Phase 1 Study of AJ1-11095 in Adults with Myelofibrosis Failed by a JAK2 Inhibitor

2025-522033-64-00 Protocol AJX-101 Human pharmacology (Phase I) - First administration to humans Authorised, recruiting

Start 26 Feb 2026 · Status Authorised, recruiting · 3 EU/EEA countries · 6 sites · Protocol AJX-101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Authorised, recruiting
Participants planned 71
Countries 3
Sites 6

Myelofibrosis

Key facts

Sponsor
Ajax Therapeutics Inc.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04], Diseases [C] - Hemic and Lymphatic Diseases [C15]
Trial duration
26 Feb 2026 → ongoing
Decision date (initial)
2026-02-09
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

External identifiers

EU CT number
2025-522033-64-00
WHO UTN
U1111-1322-0018
ClinicalTrials.gov
NCT06343805

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Myelofibrosis

VersionLevelCodeTermSystem organ class
20.0 PT 10028537 Myelofibrosis 100000004864

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Ajax Therapeutics Inc.

Sponsor organisation
Ajax Therapeutics Inc.
Address
275 Madison Avenue Floor 39th
City
New York
Postcode
10016-1132
Country
United States

Scientific contact point

Organisation
Ajax Therapeutics Inc.
Contact name
David Steensma

Public contact point

Organisation
Ajax Therapeutics Inc.
Contact name
Martin Vogelbaum

Locations

3 EU/EEA countries · 6 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ongoing, recruiting 4 1
Italy Authorised, recruitment pending 7 2
Spain Ongoing, recruiting 9 3
Rest of world
United States
51

Investigational sites

France

1 site · Ongoing, recruiting
Hopital Saint Louis
Clinical Investigation Center, 1 Avenue Claude Vellefaux, 75010, Paris

Italy

2 sites · Authorised, recruitment pending
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
Hematology, Via Francesco Sforza 35, 20122, Milan
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Hematology, Via Pietro Albertoni 15, 40138, Bologna

Spain

3 sites · Ongoing, recruiting
Hospital General Universitario Gregorio Maranon
Hematology, Calle Del Doctor Esquerdo 46, 28009, Madrid
Hospital Universitario Ramon Y Cajal
Hematology, Carretera Del Colmenar Viejo Km 9 100, Por El Pardo, Madrid
Hospital Clinic De Barcelona
Hematology, Calle Villarroel 170, 08036, Barcelona

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2026-02-26 2026-06-01
Spain 2026-03-05 2026-03-26

Application history

5 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2025-10-01 Spain Acceptable
2026-02-09
2026-02-09
2 NON SUBSTANTIAL MODIFICATION NSM-1 2026-02-19 Acceptable
2026-02-09
2026-02-19
3 NON SUBSTANTIAL MODIFICATION NSM-2 2026-02-20 2026-02-20
4 SUBSTANTIAL MODIFICATION SM-2 2026-02-20 Spain Acceptable 2026-03-03
5 NON SUBSTANTIAL MODIFICATION NSM-3 2026-03-06 Spain Acceptable 2026-03-06