A Study to Investigate ARV-027 in Healthy Male Participants and Participants with Spinal and Bulbar Muscular Atrophy

2025-523469-79-00 Protocol ARV-027-101 Human pharmacology (Phase I) - First administration to humans Ongoing, recruiting

Start 16 Jan 2026 · Status Ongoing, recruiting · 1 EU/EEA countries · 1 sites · Protocol ARV-027-101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ongoing, recruiting
Participants planned 106
Countries 1
Sites 1

Spinal and Bulbar Muscular Atrophy

Key facts

Sponsor
Arvinas Operations Inc.
Participant type
Patients, Healthy volunteers
Age range
18-64 years, 65+ years
Gender
Male
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Trial duration
16 Jan 2026 → ongoing
Decision date (initial)
2025-12-24
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Spinal and Bulbar Muscular Atrophy

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Arvinas Operations Inc.

Sponsor organisation
Arvinas Operations Inc.
Address
5 Science Park
City
New Haven
Postcode
06511-1966
Country
United States

Scientific contact point

Organisation
Arvinas Operations Inc.
Contact name
Clinical Trials NS

Public contact point

Organisation
Arvinas Operations Inc.
Contact name
Clinical Trials NS

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Netherlands Ongoing, recruiting 106 1
Rest of world 0

Investigational sites

Netherlands

1 site · Ongoing, recruiting
Centre for Human Drug Research
Neurology, Zernikedreef 8, 2333 CL, Leiden

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Netherlands 2026-01-16 2026-01-26

Application history

3 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2025-11-17 Netherlands Acceptable
2025-12-24
2025-12-24
2 SUBSTANTIAL MODIFICATION SM-1 2026-01-26 Netherlands Acceptable 2026-02-03
3 SUBSTANTIAL MODIFICATION SM-2 2026-03-11 Netherlands Acceptable
2026-03-19
2026-03-20