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2024-518006-40-00
5
2025-11-13
Early Symptomatic Alzheimer’s Disease (MCI to Mild Dementia Due to AD)
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2025-521775-31-00
5
2025-11-12
Stage IB-IIIA NSCLC Patients with uncommon EGFR Mutations
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2025-520998-39-00
5
2025-11-07
Congenital pseudarthrosis of the tibia
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2024-515926-10-00
5
2025-10-28
Paroxysmal Nocturnal Hemoglobinuria (PNH)
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2024-514974-39-00
5
2025-10-10
Developmental and Epileptic Encephalopathies (DEEs)
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2024-518645-17-00
5
2025-10-07
Blood and lymphatic diseases
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2023-508056-19-00
5
2025-10-02
HER2-Expressing (IHC 3+/IHC 2+), Mismatch Repair Proficient (pMMR), P
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2024-520196-27-00
3
2025-10-01
Rheumatoid Arthritis
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2024-518296-56-00
5
2025-09-29
Crohn’s Disease
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2022-501867-42-01
9
2025-09-08
Acute Lymphoblastic Leukemia, in Relapse
Lymphoblastic Lymphoma (Precu
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2024-520107-12-00
5
2025-09-03
Hidradenitis Suppurativa // Prurigo Nodularis // Vitiligo
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2022-501866-22-00
9
2025-08-26
Acute Lymphoblastic Leukemia, in Relapse
Lymphoblastic Lymphoma (Precu
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2024-518589-29-00
5
2025-08-21
Bronchiectasis
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2022-502910-10-00
7
2025-08-11
Propionic Acidemia
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2024-514595-41-00
5
2025-08-05
homozygous familial hypercholesterolemia
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2024-517589-41-00
1
2025-08-04
Advanced solid tumors
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2023-505479-56-00
1
2025-07-30
Follicular lymphoma (FL)
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2023-506348-17-00
4
2025-07-22
Relapsed/refractory (r/r) mature B cell neoplasms who have relapsed af
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2024-516525-31-01
5
2025-07-14
Primary Biliary Cholangitis
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2024-517968-36-00
5
2025-07-08
non-small cell lung cancer
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2024-518973-32-00
5
2025-07-03
Chronic Graft-Versus-Host Disease
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2024-512360-55-00
4
2025-06-30
Unresectable locally recurrent or metastatic hormone receptor (HR)-pos
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2024-518359-47-00
10
2025-06-17
Acute Myeloid Leukemia
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2024-515622-80-00
5
2025-06-04
Type 3 Von Willebrand Disease