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2025-523100-77-00
4
2026-04-23
Ulcerative Colitis
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2025-522878-36-00
5
2026-04-20
Chronic Spontaneous Urticaria
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2025-523234-66-00
4
2026-04-17
Well-Controlled Recurrent Pericarditis
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2024-514006-31-00
9
2026-04-16
Non-active Progressive Multiple Sclerosis (PMS)
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2024-512248-47-00
9
2026-04-15
Non-small Cell Lung Cancer (NSCLC)
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2025-521327-67-00
4
2026-04-13
Metastatic Castration-Resistant Prostate Cancer
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2025-522387-32-00
5
2026-04-10
Uveal Melanoma
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2025-521792-31-01
5
2026-04-07
Homozygous Familial Hypercholesterolemia (HoFH)
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2025-523013-28-00
4
2026-04-07
Endocrine-Resistant Hormone-Receptor-Positive, HER2-Negative Advanced
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2025-521521-33-00
10
2026-04-02
Kidney transplant rejection
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2025-522191-86-00
5
2026-04-02
Focal segmental glomerulosclerosis
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2025-522279-27-00
5
2026-04-02
Newly Diagnosed AML with an NPM1 mutation
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2025-520902-37-00
4
2026-04-01
Non-small cell lung cancer stage IV
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2025-521966-91-00
4
2026-03-31
Refractory Metastatic Breast Cancer with Liver Dominant Disease
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2024-519578-38-00
10
2026-03-30
Classic congenital adrenal hyperplasia
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2025-521142-22-00
5
2026-03-27
Hereditary Angioedema
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2025-523204-68-00
4
2026-03-25
HER2-positive breast cancer
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2025-522892-27-00
4
2026-03-21
Bronchiectasis
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2025-521314-25-00
5
2026-03-19
NPM1-m and KMT2A-r Acute Myeloid Leukemia
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2025-521884-12-00
5
2026-03-19
First line triple-negative breast cancer (TNBC)
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2024-519555-28-00
5
2026-03-18
Dravet syndrome
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2025-522361-30-00
5
2026-03-17
Primary Mitochondrial Disease, Mitochondrial DNA 3243A>G variant and A
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2025-521858-42-00
5
2026-03-16
Hemophilia
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2025-522492-28-00
4
2026-03-13
AChR-Ab Seropositive Generalized Myasthenia Gravis, Myasthenia Gravis,