-
2025-520624-25-00
10
2025-09-19
Secondary Hemophagocytic Lymphohistiocytosis (sHLH)
-
2022-501867-42-01
9
2025-09-08
Acute Lymphoblastic Leukemia, in Relapse
Lymphoblastic Lymphoma (Precu
-
2022-501866-22-00
9
2025-08-26
Acute Lymphoblastic Leukemia, in Relapse
Lymphoblastic Lymphoma (Precu
-
2024-518589-29-00
5
2025-08-21
Bronchiectasis
-
2022-502910-10-00
7
2025-08-11
Propionic Acidemia
-
2024-512753-24-00
5
2025-08-05
Acute Myeloid Leukemia (AML)
-
2023-506348-17-00
4
2025-07-22
Relapsed/refractory (r/r) mature B cell neoplasms who have relapsed af
-
2024-517968-36-00
5
2025-07-08
non-small cell lung cancer
-
2024-518973-32-00
5
2025-07-03
Chronic Graft-Versus-Host Disease
-
2023-505946-24-00
5
2025-05-15
Primary Immunodeficiency Diseases
-
2024-512733-32-00
5
2025-03-31
Acute Myeloid Leukemia (AML)
-
2024-511346-39-00
3
2025-03-28
Immune-mediated necrotizing myopathy
-
2024-513018-36-00
5
2025-03-06
Lung Diseases, Interstitial
-
2024-512536-29-00
4
2025-02-28
Amyotrophic Lateral Sclerosis (ALS)
-
2023-506537-29-00
5
2025-02-24
Haemophilia A
-
2024-513317-12-00
5
2025-02-05
Pancreatic cancer
-
2023-507843-12-01
5
2025-01-24
Refractory Epilepsy
-
2024-517410-15-01
5
2025-01-14
Rectal cancer
-
2024-513356-15-00
5
2024-12-30
Acquired Blepharoptosis
-
2024-513077-48-00
5
2024-12-19
O6-methylguanine methyltransferase (MGMT) unmethylated glioblastoma
-
2024-511190-30-00
4
2024-11-25
Short-coupled Idiopathic Ventricular Fibrillation
-
2023-503630-44-00
10
2024-11-20
Treatment of moderate-to-severe Atopic dermatitis
-
2023-504231-41-01
10
2024-10-02
Locally advanced or metastatic urothelial cancer
-
2023-507129-40-00
4
2024-08-06
interstitial lung disease secondary to systemic sclerosis (SSc-ILD)