NoticeThis is an independent non-profit initiative. We are not affiliated with the European Medicines Agency (EMA) or the official CTIS system. For the official EU Clinical Trials Information System, visit:
EMA Registry →
Friedreich’s ataxia is the most common inherited ataxia in humans and results from a deficiency
of the mitochondrial protein, FXN. Friedreich’s ataxia is a rare, progressive, multisystem disease
with an incidence that is estimated to be 1:29,000, and a carrier frequency of ~1:85.
1 total trials
Filter these 1 trials by phase, country, sponsor and more.