Study of HRO761 alone or in combination in cancer patients with specific DNA alterations called Microsatellite Instability-High or Mismatch Repair Deficiency

2022-502314-93-00 Protocol CHRO761A12101 Human pharmacology (Phase I) - First administration to humans Ongoing, recruitment ended

Start 5 Feb 2024 · Status Ongoing, recruitment ended · 7 EU/EEA countries · 15 sites · Protocol CHRO761A12101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ongoing, recruitment ended
Participants planned 329
Countries 7
Sites 15

MSIhi or dMMR advanced unresectable or metastatic solid tumors

Key facts

Sponsor
Novartis Pharma AG
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
5 Feb 2024 → ongoing
Decision date (initial)
2023-09-19
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

External identifiers

EU CT number
2022-502314-93-00
ClinicalTrials.gov
NCT05838768

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

MSIhi or dMMR advanced unresectable or metastatic solid tumors

VersionLevelCodeTermSystem organ class
21.0 LLT 10080676 Microsatellite instability 10010331
20.0 PT 10077888 Mismatch repair cancer syndrome 100000004850
20.1 PT 10079618 Microsatellite instability cancer 100000004864

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Novartis Pharma AG

Sponsor organisation
Novartis Pharma AG
Address
Lichtstrasse 35
City
Basel Town
Postcode
4056
Country
Switzerland

Scientific contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Public contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Locations

7 EU/EEA countries · 15 investigational sites

By country

CountryMS statusPlanned subjectsSites
Belgium Ongoing, recruitment ended 16 1
France Ongoing, recruitment ended 40 3
Germany Ended 46 3
Italy Ongoing, recruitment ended 30 2
Norway Ongoing, recruitment ended 12 1
Spain Ongoing, recruitment ended 32 4
Sweden Ongoing, recruitment ended 8 1
Rest of world
Israel, Taiwan, Singapore, China, United States, Japan, Korea, Republic of, United Kingdom
145

Investigational sites

Belgium

1 site · Ongoing, recruitment ended
Cliniques Universitaires Saint-Luc
#1100: Medical Oncology, Hippokrateslaan 10, Batiment 54, Sint-Lambrechts-Woluwe

France

3 sites · Ongoing, recruitment ended
Oncopole Claudius Regaud
1204: Oncologie Médicale, 1 Avenue Irene Joliot Curie, 31100, Toulouse
Institut Paoli-Calmettes
1201: Oncologie Médicale, 232 Boulevard De Sainte Marguerite, Bp 156, Marseille
Institut Bergonie
1200: Oncologie Médicale, 229 Cours De L Argonne, 33000, Bordeaux

Germany

3 sites · Ended
Universitaetsklinikum Ulm AöR
#1302: Comprehensiv Cancer Center Ulm (CCCU) / Early Clinical Trial Unit (ECTU), Albert-Einstein-Allee 23, Eselsberg, Ulm
Universitaetsklinikum Jena KöR
#1303: Abteilung Hämatologie und Internistische Onkologie​​, Am Klinikum 1, Lobeda, Jena
Universitaetsklinikum Essen AöR
#1300: Innere Klinik (Tumorforschung), Hufelandstrasse 55, Holsterhausen, Essen

Italy

2 sites · Ongoing, recruitment ended
ASST Grande Ospedale Metropolitano Niguarda
#1500: SC. Oncologia Medica FALCK Niguarda Cancer center, Piazza Dell'ospedale Maggiore 3, 20162, Milan
Humanitas Research Hospital
#1501: U.O. Oncologia Medica ed Ematologia, Via Alessandro Manzoni 56, 20089, Rozzano

Norway

1 site · Ongoing, recruitment ended
Oslo University Hospital HF
#1600: Department of Oncology, Montebello, Ullernchausséen 70, Oslo

Spain

4 sites · Ongoing, recruitment ended
Hospital Universitari Vall D Hebron
#1701: Oncologia, Edificio Materno-Infantil, Passeig De La Vall D'hebron 119-129, Barcelona
Instituto de Investigacion Sanitaria Fundacion para la Investigacion del Hospital Clinico de Valencia-INCLIVA
#1700: Oncologia, Avenida Menendez Y Pelayo 4 Acc, 46010, Valencia
Hospital General Universitario Gregorio Maranon
#1702: Oncologia, Calle Del Doctor Esquerdo 46, 28009, Madrid
Hospital Universitario Fundacion Jimenez Diaz
#1703: Oncologia, Avenida De Los Reyes Catolicos 2, 28040, Madrid

Sweden

1 site · Ongoing, recruitment ended
Karolinska University Hospital
#1800: Fas 1-enheten, Centrum för Kliniska Cancerstudier, “-“, 171 76, Stockholm

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Belgium 2024-09-04 2024-09-04 2026-01-26
France 2024-03-08 2024-03-08 2026-01-09
Germany 2024-02-05 2024-02-05 2025-09-11
Italy 2024-05-21 2024-05-21 2025-10-23
Norway 2024-08-01 2024-08-01 2025-08-06
Spain 2024-04-12 2024-04-12 2025-11-28
Sweden 2024-08-07 2024-08-07 2025-10-22

Application history

7 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-05-25 France Acceptable
2023-09-18
2023-09-19
2 SUBSTANTIAL MODIFICATION SM-1 2023-10-24 France Acceptable
2024-01-10
2024-01-11
3 SUBSTANTIAL MODIFICATION SM-2 2024-08-07 France Acceptable
2024-10-07
2024-10-07
4 SUBSTANTIAL MODIFICATION SM-3 2025-01-31 France Acceptable
2025-04-02
2025-04-02
5 SUBSTANTIAL MODIFICATION SM-4 2025-04-11 France Acceptable 2025-05-06
6 SUBSTANTIAL MODIFICATION SM-5 2025-06-11 France Acceptable
2025-08-07
2025-08-07
7 SUBSTANTIAL MODIFICATION SM-6 2025-12-09 France Acceptable
2026-03-11
2026-03-11