A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of Multiple-Ascending Doses of RO7303509 in Patients with Systemic Sclerosis

2022-502981-26-00 Protocol GA43360 Human pharmacology (Phase I) - Other Ended

Start 27 Jun 2022 · End 11 Jul 2025 · Status Ended · 6 EU/EEA countries · 16 sites · Protocol GA43360

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Ended
Participants planned 100
Countries 6
Sites 16

Systemic Sclerosis

Key facts

Sponsor
Genentech Inc.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Phenomena and Processes [G] - Physical Phenomena [G01], Diseases [C] - Immune System Diseases [C20], Diseases [C] - Skin and Connective Tissue Diseases [C17], Diseases [C] - Respiratory Tract Diseases [C08], Phenomena and Processes [G] - Immune System Phenomena [G13]
Trial duration
27 Jun 2022 → 11 Jul 2025
Decision date (initial)
2024-02-23
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

External identifiers

EU CT number
2022-502981-26-00
EudraCT number
2021-004578-68

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Systemic Sclerosis

VersionLevelCodeTermSystem organ class
21.0 LLT 10042953 Systemic sclerosis 10028395

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Genentech Inc.

Sponsor organisation
Genentech Inc.
Address
1 Dna Way
City
South San Francisco
Postcode
94080-4990
Country
United States

Scientific contact point

Organisation
Genentech Inc.
Contact name
US Program Manager Product Development Regulatory

Public contact point

Organisation
Genentech Inc.
Contact name
US Program Manager Product Development Regulatory

Locations

6 EU/EEA countries · 16 investigational sites

By country

CountryMS statusPlanned subjectsSites
Belgium Ended 4 1
France Ended 14 7
Germany Ended 4 1
Poland Ended 14 2
Portugal Ended 4 2
Spain Ended 12 3
Rest of world
Mexico, Israel, Argentina, United States, Serbia, United Kingdom
48

Investigational sites

Belgium

1 site · Ended
UZ Leuven
Department of Rheumatology, Herestraat 49, 3000, Leuven

France

7 sites · Ended
Centre Hospitalier Universitaire De Rennes
Service de médecine interne et immunologie clinique, 2 Rue Henri Le Guilloux, 35000, Rennes
Centre Hospitalier Universitaire De Toulouse
Service de Médecine Interne et immunologie clinique, 1 Avenue Du Professeur Jean Poulhes, Tsa 50032, Toulouse Cedex 9
Assistance Publique Hopitaux De Paris
Service de Rhumatologie, 27 Rue Du Faubourg Saint Jacques, 75014, Paris
Centre Hospitalier Universitaire De Bordeaux
Service de Rhumatologie, 12 ème étage, Place Amelie Raba Leon, 33000, Bordeaux
Les Hopitaux Universitaires De Strasbourg
Service d’immunologie clinique, 1 Place De L Hopital, Cs 80426, Strasbourg Cedex
Centre Hospitalier Universitaire Grenoble Alpes
Service de médecine vasculaire Boulevard de la Chantourne, Boulevard De La Chantourne, Cs 10217, Grenoble Cedex 9
Assistance Publique Hopitaux De Paris
Service de Médecine Interne, 27 Rue Du Faubourg Saint Jacques, 75014, Paris

Germany

1 site · Ended
Medical Center - University Of Freiburg
Clinic of Rheumatology and Clinical Immunology, Hugstetter Strasse 55, Stuehlinger, Freiburg Im Breisgau

Poland

2 sites · Ended
Szpital Uniwersytecki Nr 2 Im Dr Jana Biziela W Bydgoszczy
Klinika Reumatologii i Układowych Chorób Tkanki Łącznej, Ul. Kornela Ujejskiego 75, 85-168, Bydgoszcz
Reumed Sp. z o.o.
Zespół Poradni Specjalistycznych REUMED, Ul. Konrada Wallenroda 2f/4, 20-607, Lublin

Portugal

2 sites · Ended
Unidade Local De Saude De Almada-Seixal E.P.E.
Rheumatology, Avenida Torrado Da Silva, 2805-267, Almada
Unidade Local De Saude De Coimbra E.P.E.
Rheumatology, Praceta Professor Mota Pinto, 3004-561, Coimbra

Spain

3 sites · Ended
Hospital Quironsalud Infanta Luisa
Rheumatology, Calle De San Jacinto 87, 41010, Sevilla
Hospital Universitari Vall D Hebron
Systemic Autoimmune Diseases, Edificio Materno-Infantil, Passeig De La Vall D'hebron 119-129, Barcelona
Hospital De La Santa Creu I Sant Pau
Rheumatology, Calle De San Antonio Maria Claret 167, 08025, Barcelona

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Belgium 2022-11-25 2023-08-31 2024-04-18
France 2022-10-03 2023-03-30 2024-06-28
Germany 2023-02-23 2024-05-07
Poland 2022-10-05 2022-12-21 2024-06-05
Portugal 2023-03-26 2025-01-09 2023-08-23 2024-06-19
Spain 2022-06-27 2022-12-19 2024-04-23

Application history

4 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-01-15 Spain Acceptable
2024-02-19
2024-02-19
2 SUBSTANTIAL MODIFICATION SM-1 2024-08-09 Spain Acceptable
2024-10-01
2024-10-04
3 SUBSTANTIAL MODIFICATION SM-2 2024-10-31 Spain Acceptable
2025-01-16
2025-01-16
4 NON SUBSTANTIAL MODIFICATION NSM-1 2025-03-27 Spain Acceptable
2025-01-16
2025-03-27