A Phase 1B, Multicenter, Randomized, Placebo- Controlled, Double-Blind Study to Evaluate the Safety, Tolerability, and Biological Activity of TQS-168 in Subjects with Amyotrophic Lateral Sclerosis

2023-504746-54-00 Protocol TQS-168-ALS-101 Human pharmacology (Phase I) - Other Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 1 sites · Protocol TQS-168-ALS-101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Authorised, recruitment pending
Participants planned 16
Countries 1
Sites 1

AMYOTROPHIC LATERAL SCLEROSIS

Key facts

Sponsor
Tranquis Therapeutics Inc.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Decision date (initial)
2023-10-11
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

External identifiers

EU CT number
2023-504746-54-00
WHO UTN
U1111-1290-3098

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

AMYOTROPHIC LATERAL SCLEROSIS

VersionLevelCodeTermSystem organ class
21.1 PT 10002026 Amyotrophic lateral sclerosis 100000004852

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Tranquis Therapeutics Inc.

Sponsor organisation
Tranquis Therapeutics Inc.
Address
3 Lagoon Drive Suite 130
City
Redwood City
Postcode
94065-1566
Country
United States

Scientific contact point

Organisation
Tranquis Therapeutics Inc.
Contact name
Rauno Oja

Public contact point

Organisation
Tranquis Therapeutics Inc.
Contact name
Rauno Oja

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Latvia Authorised, recruitment pending 16 1
Rest of world 0

Investigational sites

Latvia

1 site · Authorised, recruitment pending
Pauls Stradins Clinical University Hospital
Neurology, Dzirciema Iela 16, 1007, Riga

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-06-27 Latvia Acceptable
2023-10-09
2023-10-11