Therapeutic approach of repeated transient blood-brain barrier opening in amyotrophic lateral sclerosis

2024-513471-40-00 Protocol APHP230845 Phase I and Phase II (Integrated) - Other Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 3 sites · Protocol APHP230845

Overview

Sponsor-declared trial summary

Phase Phase I and Phase II (Integrated) - Other
Status Authorised, recruitment pending
Participants planned 23
Countries 1
Sites 3

Amyotrophic lateral Sclerosis

Key facts

Sponsor
Assistance Publique Hopitaux De Paris
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Decision date (initial)
2025-03-19
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Amyotrophic lateral Sclerosis

VersionLevelCodeTermSystem organ class
20.0 SOC 10029205 Nervous system disorders 8
21.1 PT 10002026 Amyotrophic lateral sclerosis 100000004852

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Assistance Publique Hopitaux De Paris

Sponsor organisation
Assistance Publique Hopitaux De Paris
Address
Porte 23, 1 Avenue Claude Vellefaux 1 Avenue Claude Vellefaux
City
Paris Cedex 10
Postcode
75475
Country
France

Scientific contact point

Organisation
Assistance Publique Hopitaux De Paris
Contact name
Coordinating Investigator

Public contact point

Organisation
Assistance Publique Hopitaux De Paris
Contact name
Coordinating Investigator

Locations

1 EU/EEA country · 3 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Authorised, recruitment pending 23 3
Rest of world 0

Investigational sites

France

3 sites · Authorised, recruitment pending
Assistance Publique Hopitaux De Paris
Neurology DepartmentClinical Investigation Center, 43 Boulevard De L Hopital, 75013, Paris
Assistance Publique Hopitaux De Paris
Neurology Department, 43 Boulevard De L Hopital, 75013, Paris
Assistance Publique Hopitaux De Paris
Neurosurgery, 43 Boulevard De L Hopital, 75013, Paris

Application history

4 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-12-06 France Acceptable
2025-03-17
2025-03-19
2 SUBSTANTIAL MODIFICATION SM-1 2025-05-13 France Acceptable
2025-06-17
2025-07-08
3 SUBSTANTIAL MODIFICATION SM-3 2026-02-23 France Acceptable with conditions
2026-04-07
2026-04-10
4 NON SUBSTANTIAL MODIFICATION NSM-1 2026-05-13 France Acceptable with conditions
2026-04-07
2026-05-13