Studies to gain insight how the drugs PCSK9-inhibitors and statins affect cholesterol and bile acid metabolism

2023-505726-34-02 Therapeutic use (Phase IV) Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 1 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic use (Phase IV)
Status Authorised, recruitment pending
Participants planned 8
Countries 1
Sites 1

Healthy volunteers

To learn more about the effects of the drugs statin (atorvastatin) and PCSK9 inhibitors (evolocumab) on the metabolism of cholesterol and bile acids in the human body.

Key facts

Sponsor
Karolinska University Hospital
Participant type
Healthy volunteers
Age range
18-64 years
Gender
Male
Therapeutic area
Phenomena and Processes [G] - Metabolism [G03]
Decision date (initial)
2024-04-12
Transition trial
No
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
No
Funding sources
Region Stockholm/ALF · Hjärt-Lungfonden · Amgen AB

External identifiers

EU CT number
2023-505726-34-02
ClinicalTrials.gov
NCT06140095

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Pharmacodynamic

To learn more about the effects of the drugs statin (atorvastatin) and PCSK9 inhibitors (evolocumab) on the metabolism of cholesterol and bile acids in the human body.

Conditions and MedDRA coding

Healthy volunteers

Regulatory references

Plan to share IPD
No
IPD plan description
Individual participant data will not be shared. Results will be published by the investigators in academic journals.
EU CT numberTitleSponsor
2023-505726-34-01 Studies to gain insight how the drugs PCSK9-inhibitors and statins affect cholesterol and bile acid metabolism Karolinska University Hospital
2023-505726-34-00 Studies to gain insight how the drugs PCSK9-inhibitors and statins affect cholesterol and bile acid metabolism Karolinska University Hospital

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 2

  1. 18-64 year old
  2. Male

Exclusion criteria 14

  1. Cardiovascular disease
  2. Cerebrovascular disease (e.g. stroke, prior aneurysm)
  3. Pulmonary disease (e.g. pulmonary hypertension, COPD)
  4. Metabolic disease (incl. but not limited to Cushing disease, Diabetes)
  5. Renal disease (by CKD criteria)
  6. Active inflammatory bowel syndrome
  7. Cancer
  8. Pregnancy
  9. Smoker
  10. Any chronic medication use
  11. Steroid treatment for the last six months or HRT
  12. Coagulopathy
  13. Musculoskeletal or neurologic disease
  14. Inclusion in any other concurrent medical research study

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Changes in the measured parameters of cholesterol and bile acid metabolism

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 2

Evolocumab

SUB128552 · Substance

Active substance
Evolocumab
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
SUBCUTANEOUS INJECTION
Max daily dose
1 U unit(s)
Max total dose
2 U unit(s)
Max treatment duration
2 Week(s)
Authorisation status
Authorised
ATC code
- — -
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Atorvastatin

SUB05600MIG · Substance

Active substance
Atorvastatin
Pharmaceutical form
TABLET
Route of administration
ORAL
Max daily dose
40 mg milligram(s)
Max total dose
400 mg milligram(s)
Max treatment duration
2 Week(s)
Authorisation status
Authorised
ATC code
- — -
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Karolinska University Hospital

Sponsor organisation
Karolinska University Hospital
Address
Halsovagen, Flemingsberg Flemingsberg
City
Huddinge
Postcode
141 86
Country
Sweden

Scientific contact point

Organisation
Karolinska University Hospital
Contact name
Mats Eriksson

Public contact point

Organisation
Karolinska University Hospital
Contact name
Mats Eriksson

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Sweden Authorised, recruitment pending 8 1
Rest of world 0

Investigational sites

Sweden

1 site · Authorised, recruitment pending
Karolinska University Hospital
Endocrinology Huddinge sjukhus, Halsovagen, Flemingsberg, Huddinge

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 9 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) Project plan PCSK9 inhib EPM 241119 1
Protocol (for publication) Provningsprotokoll FINAL 241119 no mark 1
Protocol (for publication) Provningsprotokoll FINAL 241119 signerad 1
Recruitment arrangements (for publication) recruitment 1
Subject information and informed consent form (for publication) 2 Samtyckesblankett EPM mall 221021 1
Subject information and informed consent form (for publication) FPI 241112 1
Subject information and informed consent form (for publication) FPI 241112 markup 1
Summary of Product Characteristics (SmPC) (for publication) 5 - Bipacksedel Atorvastatin 1
Summary of Product Characteristics (SmPC) (for publication) 5 - Bipacksedel Evolocumab 1

Application history

2 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-01-31 Sweden Acceptable
2024-04-11
2024-04-12
2 SUBSTANTIAL MODIFICATION SM-2 2024-12-03 Sweden Acceptable
2025-01-14
2025-03-10