PRAISE-MR trial

2023-506634-70-00 Therapeutic use (Phase IV) Ended

Start 29 Feb 2024 · End 10 Mar 2026 · Status Ended · 1 EU/EEA countries · 2 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic use (Phase IV)
Status Ended
Participants planned 110
Countries 1
Sites 2

Heart failure with preserved ejection fraction Secundary mitral valve regurgitation

The main objective of this study is to assess the hemodynamic effects of sacubitril-valsartan in patients with HFpEF and secondary / atrial functional mitral regurgitation (AFMR), using a combination of cardiopulmonary exercise testing and stress echocardiography (referred to as CPETecho). Secondary endpoints include t…

Key facts

Sponsor
Ziekenhuis Oost Limburg
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Cardiovascular Diseases [C14]
Trial duration
29 Feb 2024 → 10 Mar 2026
Decision date (initial)
2023-10-11
Transition trial
No
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Therapy

The main objective of this study is to assess the hemodynamic effects of sacubitril-valsartan in patients with HFpEF and secondary / atrial functional mitral regurgitation (AFMR), using a combination of cardiopulmonary exercise testing and stress echocardiography (referred to as CPETecho). Secondary endpoints include the changes in quantitative valve assessment (EROA), quality of life and different CPETecho parameters.

Conditions and MedDRA coding

Heart failure with preserved ejection fraction Secundary mitral valve regurgitation

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 1

  1. (1) Age > 18 years (2) NYHA class II to IV (3) Written informed consent (4) Left ventricular ejection fraction ≥ 50% (5) Objective evidence of cardiac structural and/or functional abnormalities consistent with the presence of LV diastolic dysfunction/raised LV filling pressures*, including raised natriuretic peptides** (6) ≥ moderate functional MR assessed by TTE within the previous year

Exclusion criteria 1

  1. (1) Systolic blood pressure < 100 mmHg (2) Potassium ≥ 5.2 mmol/L (3) eGFR ≤ 25 ml/min/1.73m² (4) History of angioedema or unacceptable side effects during receipt of ACE inhibitors or ARBs (5) Structural mitral valve disease and previous or planned mitral valve intervention (6) Already receiving ARNI (sacubitril-valsartan) therapy (7) Severe comorbid condition limiting life expectancy < 24 months or inability to perform a maximal CPETecho

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Change in the mPAP/CO slope between randomization and 6 months thereafter

Secondary endpoints 1

  1. Changes in (1) Peak VO2 (2) Mitral effective regurgitant orifice area (EROA) (3) Natriuretic peptide levels (NTproBNP) (4) Left atrial volume (Left Atrial Volume Index, LAVI) (5) Left atrial function (Peak Atrial Longitudinal Strain, PALS) (6) VE/VCO2 slope (7) Patient reported outcomes (Kansas City Cardiomyopathy Questionnaire, KCCQ-12)

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 3

Entresto 49 mg/51 mg film-coated tablets

PRD3417302 · Product

Active substance
Valsartan
Pharmaceutical form
FILM-COATED TABLET
Route of administration
ORAL
Max daily dose
194 mg milligram(s)
Max total dose
194 mg milligram(s)
Max treatment duration
6 Month(s)
Authorisation status
Authorised
ATC code
C09DX04 — -
Marketing authorisation
EU/1/15/1058/002
MA holder
NOVARTIS EUROPHARM LIMITED
MA country
EU
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Entresto 24 mg/26 mg film-coated tablets

PRD3417298 · Product

Active substance
Valsartan
Pharmaceutical form
FILM-COATED TABLET
Route of administration
ORAL
Max daily dose
194 mg milligram(s)
Max total dose
194 mg milligram(s)
Max treatment duration
6 Month(s)
Authorisation status
Authorised
ATC code
C09DX04 — -
Marketing authorisation
EU/1/15/1058/001
MA holder
NOVARTIS EUROPHARM LIMITED
MA country
EU
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Entresto 97 mg/103 mg film-coated tablets

PRD3417299 · Product

Active substance
Valsartan
Pharmaceutical form
FILM-COATED TABLET
Route of administration
ORAL
Max daily dose
194 mg milligram(s)
Max total dose
194 mg milligram(s)
Max treatment duration
6 Month(s)
Authorisation status
Authorised
ATC code
C09DX04 — -
Marketing authorisation
EU/1/15/1058/005
MA holder
NOVARTIS EUROPHARM LIMITED
MA country
EU
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Ziekenhuis Oost Limburg

Sponsor organisation
Ziekenhuis Oost Limburg
Address
Synaps Park 1
City
Genk
Postcode
3600
Country
Belgium

Scientific contact point

Organisation
Ziekenhuis Oost Limburg
Contact name
Clinical Trial Unit

Public contact point

Organisation
Ziekenhuis Oost Limburg
Contact name
Clinical Trial Unit

Locations

1 EU/EEA country · 2 investigational sites

By country

CountryMS statusPlanned subjectsSites
Belgium Ended 110 2
Rest of world 0

Investigational sites

Belgium

2 sites · Ended
Jessa Ziekenhuis
Cardiology, Stadsomvaart 11, 3500, Hasselt
Ziekenhuis Oost Limburg
Cardiology, Synaps Park 1, 3600, Genk

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Belgium 2024-02-29 2026-03-10 2024-02-29 2025-09-24

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-07-17 Belgium Acceptable
2023-10-11
2023-10-11