Differences in coagulation between fresh frozen plasma and Solvent-detergent plasma in pediatric congenital heart surgery.

2024-514073-22-01 Therapeutic confirmatory (Phase III) Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 1 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic confirmatory (Phase III)
Status Authorised, recruitment pending
Participants planned 120
Countries 1
Sites 1

Coagulation in pediatric cardiac surgery

To investigate the differences in coagulation variables just after surgery between FFP and S/D plasma (Omniplasma) use. The main coagulation variables of interest are protein S activity and α2-ntiplasmin. Other important coagulation variables are aPTT, PT, ROTEM, fibrinolysis (measured with ROTEM) fibrinogen, Hb, throm…

Key facts

Sponsor
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Participant type
Pediatric, Patients
Age range
0-17 years
Gender
Male and Female
Therapeutic area
Diseases [C] - Hemic and Lymphatic Diseases [C15]
Decision date (initial)
2024-09-23
Transition trial
Yes
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
No

External identifiers

EU CT number
2024-514073-22-01
EudraCT number
2021-000444-22

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Others

To investigate the differences in coagulation variables just after surgery between FFP and S/D plasma (Omniplasma) use. The main coagulation variables of interest are protein S activity and α2-ntiplasmin. Other important coagulation variables are aPTT, PT, ROTEM, fibrinolysis (measured with ROTEM) fibrinogen, Hb, thrombocyte count, protein C activity, antithrombin and plasminogen.

Conditions and MedDRA coding

Coagulation in pediatric cardiac surgery

Regulatory references

Plan to share IPD
No
EU CT numberTitleSponsor
2024-514073-22-00 Differences in coagulation between fresh frozen plasma and Solvent-detergent plasma in pediatric congenital heart surgery Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 4

  1. Informed consent
  2. Cardiac surgery with the use of CPB
  3. Group 1A and Group 2A children < 1 year old
  4. Group 1B and Group 2B Glenn / Fontan surgery

Exclusion criteria 4

  1. No informed consent
  2. Cardiac surgery without the use of CPB
  3. Preoperative known coagulation disorders
  4. Known allergy for FFP or Omniplasma

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Primary outcome involves the difference of coagulation variables measured just after surgery between FFP or Omniplasma use. The coagulation variables of interest are protein C activity, protein S activity, α2-antiplasmin, antithrombin, plasminogen, Hb, thrombocyte count, ROTEM, aPTT, PT and fibrinogen.

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Plasma

SUB118891 · Substance

Active substance
Plasma
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
INTRAVENOUS INFUSION
Max daily dose
3500
Max total dose
3500
Max treatment duration
1 Week(s)
Authorisation status
Authorised
ATC code
- — -
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Comparator 1

Omniplasma 45-70 mg/ml oplossing voor infusie

PRD311829 · Product

Active substance
Human Plasma Protein
Pharmaceutical form
SOLUTION FOR INFUSION
Route of administration
INFUSION
Max daily dose
3500 ml millilitre(s)
Max total dose
3500 ml millilitre(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
B05AA — BLOOD SUBSTITUTES AND PLASMA PROTEIN FRACTIONS
Marketing authorisation
RVG 25407
MA holder
OCTAPHARMA GMBH
MA country
Netherlands
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)

Sponsor organisation
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Address
Dr. Molewaterplein 40
City
Rotterdam
Postcode
3015 GD
Country
Netherlands

Scientific contact point

Organisation
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Contact name
Research office Cardiothoracic Surgery

Public contact point

Organisation
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Contact name
Research office Cardiothoracic Surgery

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Netherlands Authorised, recruitment pending 120 1
Rest of world 0

Investigational sites

Netherlands

1 site · Authorised, recruitment pending
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Anesthesiology, Dr. Molewaterplein 40, 3015 GD, Rotterdam

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 7 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1_Protocol 2024-514073-22-01 4
Recruitment arrangements (for publication) Blank document for CTIS submission 1
Subject information and informed consent form (for publication) L1_SIS and ICF 202100044422 3.1
Summary of Product Characteristics (SmPC) (for publication) E2_SmPC FFP 1
Summary of Product Characteristics (SmPC) (for publication) E2_SmPC Omniplasma 1
Synopsis of the protocol (for publication) D1_Protocol synopsis_ENG_2024-514073-22-01 1
Synopsis of the protocol (for publication) D1_Protocol synopsis_NL_2024-514073-22-01 1

Application history

2 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-09-04 Netherlands Acceptable with conditions
2024-09-23
2024-09-23
2 SUBSTANTIAL MODIFICATION SM-3 2026-04-01 Netherlands Acceptable
2026-05-22
2026-05-22