The use of [68Ga]Ga-FAPI PET/MRI in assessing disease activity in patients with Graves’ orbitopathy

2025-521163-12-01 Phase I and Phase II (Integrated) - Other Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 1 sites

Overview

Sponsor-declared trial summary

Phase Phase I and Phase II (Integrated) - Other
Status Authorised, recruitment pending
Participants planned 10
Countries 1
Sites 1

Graves' Orbitopathy

The main objective of this study is to compare the uptake of FAPI (Fibroblast Activation Protein Inhibitor) in patients with active Graves' Ophthalmopathy (GO) versus those with inactive GO. This comparison aims to determine the differential uptake patterns and potential diagnostic value of FAPI in assessing disease ac…

Key facts

Sponsor
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Immune System Diseases [C20], Diseases [C] - Eye Diseases [C11], Analytical, Diagnostic and Therapeutic Techniques and Equipment [E] - Diagnosis [E01]
Decision date (initial)
2025-10-30
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No
Funding sources
SWOO (Stichting Wetenschappelijk Onderzoek Het Oogziekenhuis) Prof.Dr. H.J. Flieringa

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Diagnosis

The main objective of this study is to compare the uptake of FAPI (Fibroblast Activation Protein Inhibitor) in patients with active Graves' Ophthalmopathy (GO) versus those with inactive GO. This comparison aims to determine the differential uptake patterns and potential diagnostic value of FAPI in assessing disease activity in GO patients.

Secondary objectives 5

  1. Compare FAPI uptake in patients with high vs. low levels of TSH-R-Ab.
  2. Compare FAPI uptake in patients with high vs. low serum concentrations of specific proteins related to GO activity.
  3. Compare FAPI uptake in patients with active inflammation (on standard MRI) vs. those without.
  4. Compare FAPI uptake in the right vs. left orbit in patients with unilateral or asymmetric orbitopathy.
  5. Compare FAPI uptake in patients with reduced vs. normal ocular motility.

Conditions and MedDRA coding

Graves' Orbitopathy

VersionLevelCodeTermSystem organ class
20.1 LLT 10057889 Graves' ophthalmopathy 10015919

Regulatory references

Plan to share IPD
No
EU CT numberTitleSponsor
2025-521163-12-00 The use of [68Ga]Ga-FAPI PET/MRI in assessing disease activity in patients with Graves’ orbitopathy Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 2

  1. Inclusion of 5 patients with Graves Orbitopathy (GO) and Clinical Activity Score (CAS) >3, consistent with active GO.
  2. Inclusion of 5 patients with GO who have previously undergone CAS >3, but with a current low CAS of 0 or 1 for at least 6 months (i.e. inactive GO)

Exclusion criteria 2

  1. General exclusion criteria for MRI, including (but not limited to) claustrophobia, metal-splinters in face-area, recent surgery etc.
  2. For active GO: if PET-MRI can not be performed <14 days, patient will not be included

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. FAPI uptake in active GO versus inactive GO on PET-MRI

Secondary endpoints 1

  1. Relation MRI results (edema), clinical symptoms, and lab values to FAPI-uptake on PET.

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

68GA-FAPI-46

PRD10114365 · Product

Active substance
(S-222-10-2-4-3-4-2-2-CYANO-44-DIFLUOROPYRROLIDIN-1-YL-2-OXOETHYLCARBAMOYL-QUINOLIN-6-YLMETHYLAMINO-PROPYLPIPERAZIN-1-YL-2-OXOETHYL-68GA-14710-TETRAAZACYCLODODECANE-147-TRIYLTRIACETATE
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
INTRAVENOUS
Authorisation status
Not Authorised
MA holder
RHPET
Paediatric formulation
No
Orphan designation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)

Sponsor organisation
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Address
Dr. Molewaterplein 40
City
Rotterdam
Postcode
3015 GD
Country
Netherlands

Scientific contact point

Organisation
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Contact name
Department of Radiology and Nuclear Medicine

Public contact point

Organisation
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Contact name
Department of Radiology and Nuclear Medicine

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Netherlands Authorised, recruitment pending 10 1
Rest of world 0

Investigational sites

Netherlands

1 site · Authorised, recruitment pending
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Radiologie en Nucleaire Geneeskunde, Dr. Molewaterplein 40, 3015 GD, Rotterdam

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 7 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1_Protocol 2025-521163-12-01_newversion 1
Protocol (for publication) D1_Protocol 2025-521163-12-01_TrackChanges 1
Recruitment arrangements (for publication) K1_Recruitment arrangements 1
Subject information and informed consent form (for publication) L1_SIS and ICF adults_newversion 1
Subject information and informed consent form (for publication) L1_SIS and ICF adults_trackchanges 1
Synopsis of the protocol (for publication) D1_Protocol synopsis_ENG 2025-521163-12-01 1
Synopsis of the protocol (for publication) D1_Protocol synopsis_NED 2025-521163-12-01 1

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2025-08-11 Netherlands Acceptable
2025-10-30
2025-10-30