Inhaled corticosteroids in young children with episodic wheezing: a multicenter cluster RCT

2025-522694-11-00 Protocol PaNaMa 12782 Therapeutic use (Phase IV) Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 3 sites · Protocol PaNaMa 12782

Overview

Sponsor-declared trial summary

Phase Therapeutic use (Phase IV)
Status Authorised, recruitment pending
Participants planned 285
Countries 1
Sites 3

Episodic expiratory wheezing

To assess the effectiveness of daily ICS for at least 6 weeks and bronchodilators if needed, compared with ICS and bronchodilators during symptoms and only bronchodilators during symptoms on symptom control, exacerbation frequency and quality of life in children aged 1-6 years with EEW treated in general practice, afte…

Key facts

Sponsor
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Participant type
Pediatric, Patients
Age range
0-17 years
Gender
Male and Female
Therapeutic area
Diseases [C] - Respiratory Tract Diseases [C08]
Decision date (initial)
2025-10-09
Transition trial
No
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
Yes

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Efficacy

To assess the effectiveness of daily ICS for at least 6 weeks and bronchodilators if needed, compared with ICS and bronchodilators during symptoms and only bronchodilators during symptoms on symptom control, exacerbation frequency and quality of life in children aged 1-6 years with EEW treated in general practice, after 1 and 12 months of follow-up.

Conditions and MedDRA coding

Episodic expiratory wheezing

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 2

  1. Children aged 1-6 years (age between ≥1 and <6)
  2. Visited the general practitioner or out-of-hour services, because of episodic expiratory wheezing, from a second episode onwards

Exclusion criteria 4

  1. Already known with cystic fibrosis, bronchopulmonary dysplasia or other chronic lung disease
  2. Premature birth <32 weeks
  3. Daily inhaled corticosteroids use or oral corticosteroids use within four weeks prior to inclusion
  4. Current antibiotic use for respiratory complaints

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Symptom control

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 4

Budesonide

SCP117250074 · ATC

Active substance
Budesonide
Route of administration
INHALATION
Max daily dose
400 µg microgram(s)
Max total dose
400 µg microgram(s)
Max treatment duration
12 Month(s)
Authorisation status
Authorised
ATC code
R03BA02 — BUDESONIDE
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Beclometasone Dipropionate

SCP102635494 · ATC

Active substance
Beclometasone Dipropionate
Substance synonyms
BECLOMETHASONE DIPROPIONATE, BECLOMETHASONE 17,21-DIPROPRIONATE
Route of administration
INHALATION
Max daily dose
400 µg microgram(s)
Max total dose
400 µg microgram(s)
Max treatment duration
12 Month(s)
Authorisation status
Authorised
ATC code
R03BA01 — BECLOMETASONE
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Salbutamol Sulfate

SCP111080421 · ATC

Active substance
Salbutamol Sulfate
Substance synonyms
Salbutamol hemisulfate, ALBUTEROL SULFATE, ALBUTEROL SULPHATE, SALBUTAMOL SULPHATE
Route of administration
INHALATION
Max daily dose
1600 µg microgram(s)
Max total dose
1600 µg microgram(s)
Max treatment duration
12 Month(s)
Authorisation status
Authorised
ATC code
R03AC02 — SALBUTAMOL
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Fluticasone Propionate

SCP101886959 · ATC

Active substance
Fluticasone Propionate
Substance synonyms
PF-00241939, EP104IAR-201
Route of administration
INHALATION
Max daily dose
250 µg microgram(s)
Max total dose
250 µg microgram(s)
Max treatment duration
12 Month(s)
Authorisation status
Authorised
ATC code
R03BA05 — FLUTICASONE
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)

Sponsor organisation
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Address
Dr. Molewaterplein 40
City
Rotterdam
Postcode
3015 GD
Country
Netherlands

Scientific contact point

Organisation
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Contact name
Evelien van Meel

Public contact point

Organisation
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
Contact name
Evelien van Meel

Locations

1 EU/EEA country · 3 investigational sites

By country

CountryMS statusPlanned subjectsSites
Netherlands Authorised, recruitment pending 285 3
Rest of world 0

Investigational sites

Netherlands

3 sites · Authorised, recruitment pending
Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)
General practice, Dr. Molewaterplein 40, 3015 GD, Rotterdam
Radboud universitair medisch centrum Stichting
Primary and Community Care, Geert Grooteplein Zuid 10, 6525 GA, Nijmegen
Leids Universitair Medisch Centrum (LUMC)
Public Health and Primary Care, P. O. Box 9600, 2300 RC, Leiden

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 14 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1_Protocol 2025-522694-11-00 2
Recruitment arrangements (for publication) K1_Recruitment arrangements 2
Recruitment arrangements (for publication) K2_Recruitment material_invitation from general practices 2
Recruitment arrangements (for publication) K2_Recruitment material_waiting room screen 1
Subject information and informed consent form (for publication) L1_SIS and ICF_parents_ErasmusMC 2
Subject information and informed consent form (for publication) L1_SIS and ICF_parents_LUMC 2
Subject information and informed consent form (for publication) L1_SIS and ICF_parents_RadboudUMC 2
Subject information and informed consent form (for publication) L2_Other subject information material_information leaflet children 2
Summary of Product Characteristics (SmPC) (for publication) E2_SmPC Beclometasone_ATC R03BA01 1
Summary of Product Characteristics (SmPC) (for publication) E2_SmPC Budesonide_ATC R03BA02 1
Summary of Product Characteristics (SmPC) (for publication) E2_SmPC Fluticasone_ATC R03BA05 1
Summary of Product Characteristics (SmPC) (for publication) E2_SmPC Salbutamol_ATC R03AC02 1
Synopsis of the protocol (for publication) D1_Protocol synopsis EN_2025-522694-11-00 2
Synopsis of the protocol (for publication) D1_Protocol synopsis NL_2025-522694-11-00 2

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2025-07-29 Netherlands Acceptable
2025-10-09
2025-10-09