-
2024-512577-27-00
5
2025-12-02
Chronic kidney disease in paediatric patients
-
2025-520927-26-00
5
2025-11-24
Metastatic Castration-resistant Prostate Cancer (mCRPC)
-
2025-522002-20-00
1
2025-11-20
PLN R14del Dilated Cardiomyopathy
-
2025-521511-40-00
10
2025-11-18
metastatic non-small cell lung cancer
-
2024-520409-38-00
1
2025-11-14
Eosinophilic esophagitis (EoE)
-
2025-520555-89-00
5
2025-11-14
Metastatic castration-resistant prostate cancer (mCRPC)
-
2025-521876-77-00
1
2025-11-03
Cholestatic liver disease
-
2024-519917-72-00
5
2025-10-29
Transthyretin Amyloidosis with Cardiomyopathy (ATTR Amyloidosis with C
-
2024-514693-47-01
11
2025-10-28
EGFR mutated locally advanced or metastatic non-small cell lung cancer
-
2023-509432-25-00
4
2025-10-24
Raynaud’s phenomenon
-
2025-521188-11-00
5
2025-10-15
Type 2 diabetes
-
2025-521377-14-00
4
2025-10-06
Atrial fibrillation
-
2024-516804-40-00
6
2025-09-25
Progressive Familial Intrahepatic Cholestasis
-
2024-511989-36-00
5
2025-09-24
Ewing Sarcoma
-
2025-520689-23-00
9
2025-09-22
nasopharyngeal carcinoma
-
2024-517051-12-00
4
2025-09-16
Relapsed primary large B-cel lymphoma of the central nervous system
-
2025-521158-40-00
4
2025-09-12
oesophageal cancer
-
2025-522368-34-00
1
2025-09-05
Alzheimer’s Disease
-
2024-519152-82-00
5
2025-09-03
Relapsed/Refractory Follicular Lymphoma
-
2024-518154-16-00
5
2025-08-27
non-small cell lung cancer
-
2023-510382-10-00
5
2025-08-25
HELLP syndrome
-
2024-519525-38-00
5
2025-08-22
Heart failure
-
2024-519667-18-00
6
2025-08-21
Pancreatic conditions requiring pancreaticoduodenectomy, such as pancr
-
2024-516095-15-00
1
2025-08-05
Kidney Disease