A Phase 1b, Open-Label, Multiple Ascending Dose, Multicenter Study of VRG50635 in Participants With Sporadic and Familial Amyotrophic Lateral Sclerosis Followed by Long-Term Treatment

2023-506509-21-00 Protocol VGCS-50635-002 Human pharmacology (Phase I) - Other Ended

Start 8 Mar 2024 · End 5 Aug 2025 · Status Ended · 5 EU/EEA countries · 9 sites · Protocol VGCS-50635-002

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Ended
Participants planned 58
Countries 5
Sites 9

Amyotrophic Lateral Sclerosis

Key facts

Sponsor
Verge Genomics
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Trial duration
8 Mar 2024 → 5 Aug 2025
Decision date (initial)
2024-01-22
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
Yes

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Amyotrophic Lateral Sclerosis

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Verge Genomics

Sponsor organisation
Verge Genomics
Address
131 Oyster Point Boulevard Suite 300
City
South San Francisco
Postcode
94080-2032
Country
United States

Scientific contact point

Organisation
Verge Genomics
Contact name
Sujata Sankar

Public contact point

Organisation
Verge Genomics
Contact name
Sujata Sankar

Locations

5 EU/EEA countries · 9 investigational sites

By country

CountryMS statusPlanned subjectsSites
Belgium Ended 8 1
Finland Ended 15 4
Netherlands Ended 8 1
Spain Ended 8 2
Sweden Not authorised 8 1
Rest of world
Canada
11

Investigational sites

Belgium

1 site · Ended
UZ Leuven
Neurology, Herestraat 49, 3000, Leuven

Finland

4 sites · Ended
Turku University Hospital
Neurology, Hameentie 11, 20520, Turku
Tampere University Hospital
Neuromuscular Research center, Biokatu 12 5 6, 33520, Tampere
University Of Eastern Finland
Brain research unit, P. O. Box 1627, 70211, Kuopio
Meilahti Hospital
Neurocenter, P. O. Box 340, 00029, Helsinki

Netherlands

1 site · Ended
Universitair Medisch Centrum Utrecht
Neurology, Heidelberglaan 100, 3584 CX, Utrecht

Spain

2 sites · Ended
Hospital Universitario Regional De Malaga
Neurology, Avenida De Carlos De Haya Sn, 29010, Malaga
Bellvitge University Hospital
Neurology, Carrer De La Feixa Llarga Sn, 08907, L'hospitalet De Llobregat

Sweden

1 site · Not authorised
Studieenheten Akademiskt Specialistcentrum
Neurology, Dalagatan 9, entréplan, Stockholm

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Belgium 2024-04-17 2024-04-25 2024-08-05
Finland 2024-04-24 2024-04-25 2024-07-04
Netherlands 2024-03-08 2024-03-11 2024-08-16

Application history

11 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-09-15 Netherlands Acceptable
2024-01-22
2024-01-22
2 SUBSTANTIAL MODIFICATION SM-1 2024-01-31 Netherlands Acceptable 2024-02-13
3 SUBSTANTIAL MODIFICATION SM-2 2024-01-31 Acceptable 2024-02-28
4 SUBSTANTIAL MODIFICATION SM-3 2024-01-31 Acceptable 2024-03-11
5 SUBSTANTIAL MODIFICATION SM-4 2024-02-02 Acceptable 2024-03-11
6 SUBSTANTIAL MODIFICATION SM-7 2024-04-09 Netherlands No conclusion
2024-05-28
2024-05-29
7 NON SUBSTANTIAL MODIFICATION NSM-1 2024-06-17 No conclusion
2024-05-28
2024-06-17
8 SUBSTANTIAL MODIFICATION SM-8 2024-08-29 Netherlands Acceptable
2024-10-21
2024-10-22
9 NON SUBSTANTIAL MODIFICATION NSM-2 2024-12-04 Netherlands Acceptable
2024-10-21
2024-12-04
10 SUBSTANTIAL MODIFICATION SM-9 2025-01-08 Netherlands Acceptable
2025-03-17
2025-03-17
11 NON SUBSTANTIAL MODIFICATION NSM-3 2025-07-14 Acceptable
2025-03-17
2025-07-14