Vosoritide

8 trials 4 recruiting MMusculoskeletal Orphan designation

Filter these 8 trials by condition, phase, country and more.

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8 Registered trials

4 Recruiting

3 Completed trials

1 Sponsors

6 Countries

Phase III

Phase II/III

Phase II

Phase III: 3 Phase II/III: 1 Phase II: 4

Oversight events:

1 corrective measure across 1 trial

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Indications tested

Hypochondroplasia 3 Turner's syndrome 1 Short stature homeobox gene mutation 1 Noonan syndrome 1

Sponsors using this IMP

Biomarin Pharmaceutical Inc. 8

All trials

8 total

A study of BMN 333 versus Vosoritide in Children with Achondroplasia Pending

2025-523811-12-00 Phase II/III 3 countries Biomarin Pharmaceutical Inc.
A Phase 2, Randomized, Double-Blind, Placebo-Controlled, Multicenter Study to Evaluate the Safety and Efficacy of Vosoritide in Infants and … Recruiting

2024-512261-14-00 Phase II 3 countries Biomarin Pharmaceutical Inc.
Long-Term Extension Study of Vosoritide to Treat Children with Hypochondroplasia Recruiting

2024-517238-16-00 Phase III 4 countries Biomarin Pharmaceutical Inc.
A Phase 2 Study of Vosoritide in Children With Idiopathic Short Stature Recruiting

2024-520137-74-00 Phase II 3 countries Biomarin Pharmaceutical Inc.
A Basket Study of Vosoritide in Children with Turner Syndrome, Short Stature Homeobox-Containing Gene Deficiency, and Noonan Syndrome with I… Recruiting

2024-515861-33-00 Phase II 4 countries Biomarin Pharmaceutical Inc.
An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia Ended

2023-508864-31-00 Phase III 2 countries Biomarin Pharmaceutical Inc.
A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Multicenter Study to Evaluate the Efficacy and Safety of Vosoritide in Children Wit… Ended

2024-513129-22-00 Phase III 4 countries Biomarin Pharmaceutical Inc.
A Long-term Study to Evaluate Safety, Tolerability, and Efficacy of BMN 111 in Children with Achondroplasia Ended

2023-508754-26-00 Phase II 1 country Biomarin Pharmaceutical Inc.

Showing 1–8 of 8 trials

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