A Multi-Center, Randomized, Double-Blind, Placebo-Controlled Multiple Ascending Dose Study to Evaluate the Safety and Tolerability of QRL-201 in Amyotrophic Lateral Sclerosis Followed by an Open-Label Extended Dosing Period

2022-500758-41-00 Protocol QRL-201-01 Human pharmacology (Phase I) - First administration to humans Ongoing, recruitment ended

Start 15 Aug 2023 · Status Ongoing, recruitment ended · 4 EU/EEA countries · 7 sites · Protocol QRL-201-01

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ongoing, recruitment ended
Participants planned 59
Countries 4
Sites 7

Amyotrophic lateral sclerosis

Key facts

Sponsor
Quralis Corp.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Trial duration
15 Aug 2023 → ongoing
Decision date (initial)
2023-05-22
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

External identifiers

EU CT number
2022-500758-41-00
ClinicalTrials.gov
NCT05633459

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Amyotrophic lateral sclerosis

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Quralis Corp.

Sponsor organisation
Quralis Corp.
Address
1209 North Orange Street
City
Wilmington
Postcode
19801-1120
Country
United States

Scientific contact point

Organisation
Quralis Corp.
Contact name
Bryan Boggs

Public contact point

Organisation
Quralis Corp.
Contact name
Bryan Boggs

Locations

4 EU/EEA countries · 7 investigational sites

By country

CountryMS statusPlanned subjectsSites
Belgium Ongoing, recruitment ended 9 1
Germany Ongoing, recruitment ended 11 4
Ireland Ongoing, recruitment ended 6 1
Netherlands Ongoing, recruitment ended 9 1
Rest of world
United Kingdom, Canada
24

Investigational sites

Belgium

1 site · Ongoing, recruitment ended
Katholieke Universiteit Te Leuven
Neurology, Herestraat 49, 3000, Leuven

Germany

4 sites · Ongoing, recruitment ended
Deutsches Zentrum Fuer Neurodegenerative Erkrankungen e.V.
Neurodegenerative Erkrankung, Venusberg-Campus 1/99, Venusberg, Bonn
University Medical Centre Schleswig-Holstein
Campus Lübeck, Neurologie, Ratzeburger Allee 160, 23538, Lübeck
Universitatsklinikum Ulm AöR
Neurology, Oberer Eselsberg 45, Eselsberg, Ulm
Charite Research Organisation GmbH
Neurologie, Neurochirurgie und Psychiatrie, Chariteplatz 1, Mitte, Berlin

Ireland

1 site · Ongoing, recruitment ended
St James's Hospital
Neurology, James's Street, Ireland, Dublin 8

Netherlands

1 site · Ongoing, recruitment ended
University Medical Center Utrecht
Neurology, Heidelberglaan 100, 3584 CX, Utrecht

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Belgium 2025-02-19 2025-02-19 2025-08-14
Germany 2023-08-16 2023-08-17 2025-08-14
Ireland 2023-08-15 2023-08-28 2025-08-14
Netherlands 2023-08-15 2023-08-17 2025-08-14

Application history

19 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-01-31 Germany Acceptable with conditions
2023-05-22
2023-05-22
2 NON SUBSTANTIAL MODIFICATION NSM-1 2023-06-09 Germany Acceptable with conditions
2023-05-22
2023-06-09
3 NON SUBSTANTIAL MODIFICATION NSM-2 2023-06-23 Germany Acceptable with conditions
2023-05-22
2023-06-23
4 SUBSTANTIAL MODIFICATION SM-12 2023-06-30 Acceptable with conditions 2023-08-24
5 SUBSTANTIAL MODIFICATION SM-13 2023-06-30 Acceptable with conditions 2023-07-19
6 SUBSTANTIAL MODIFICATION SM-14 2023-06-30 Acceptable with conditions 2023-08-01
7 SUBSTANTIAL MODIFICATION SM-15 2023-06-30 Germany Acceptable with conditions 2023-09-18
8 SUBSTANTIAL MODIFICATION SM-16 2024-06-12 Germany Acceptable
2024-09-12
2024-09-12
9 NON SUBSTANTIAL MODIFICATION NSM-3 2024-09-24 Acceptable
2024-09-12
2024-09-24
10 SUBSTANTIAL MODIFICATION SM-17 2024-09-27 Acceptable
2025-01-13
2025-01-13
11 SUBSTANTIAL MODIFICATION SM-18 2025-01-27 Germany Acceptable
2025-01-29
2025-01-29
12 NON SUBSTANTIAL MODIFICATION NSM-4 2025-01-31 Acceptable
2025-01-29
2025-01-31
13 SUBSTANTIAL MODIFICATION SM-19 2025-01-31 Germany Acceptable 2025-02-06
14 NON SUBSTANTIAL MODIFICATION NSM-5 2025-02-07 Germany 2025-02-07
15 NON SUBSTANTIAL MODIFICATION NSM-6 2025-02-19 Germany 2025-02-19
16 SUBSTANTIAL MODIFICATION SM-20 2025-05-16 Germany Acceptable
2025-08-06
2025-08-07
17 NON SUBSTANTIAL MODIFICATION NSM-7 2025-09-01 Acceptable
2025-08-06
2025-09-01
18 SUBSTANTIAL MODIFICATION SM-21 2025-10-30 Acceptable 2025-12-15
19 SUBSTANTIAL MODIFICATION SM-22 2026-01-30 Germany Acceptable
2026-02-27
2026-03-04